Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1

Marfan syndrome (MFS) is a heritable dominant disorder of fibrous connective tissue, caused by mutations in the gene encoding fibrillin-1 on chromosome 15. Here, we report an induced pluripotent stem cell (iPSC) line generated from a patient with MFS who carries a heterozygous mutation of c.2777G &g...

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Main Authors: Ronghua Liu, Guoxing Weng, Fuzhen Zheng, Jinyan Chen, Kun Wang, Junyong Han, Jie Huang, Licheng Yan, Jingjun Jin
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Stem Cell Research
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506124002897
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author Ronghua Liu
Guoxing Weng
Fuzhen Zheng
Jinyan Chen
Kun Wang
Junyong Han
Jie Huang
Licheng Yan
Jingjun Jin
author_facet Ronghua Liu
Guoxing Weng
Fuzhen Zheng
Jinyan Chen
Kun Wang
Junyong Han
Jie Huang
Licheng Yan
Jingjun Jin
author_sort Ronghua Liu
collection DOAJ
description Marfan syndrome (MFS) is a heritable dominant disorder of fibrous connective tissue, caused by mutations in the gene encoding fibrillin-1 on chromosome 15. Here, we report an induced pluripotent stem cell (iPSC) line generated from a patient with MFS who carries a heterozygous mutation of c.2777G > A(p.Cys926Tyr) in the FBN1 gene using an episomal method. The hiPS-MFS cell line has normal karyotype, expresses pluripotency markers, and has the ability to form three germ layers in vivo.This MFS-specific iPSC line can be used as a cell disease model to study the pathogenesis of Marfan syndrome.
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institution DOAJ
issn 1873-5061
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publishDate 2024-12-01
publisher Elsevier
record_format Article
series Stem Cell Research
spelling doaj-art-6bbfe0958c034a28af4e581afe5b58302025-08-20T02:49:53ZengElsevierStem Cell Research1873-50612024-12-018110359110.1016/j.scr.2024.103591Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1Ronghua Liu0Guoxing Weng1Fuzhen Zheng2Jinyan Chen3Kun Wang4Junyong Han5Jie Huang6Licheng Yan7Jingjun Jin8Fujian Key Laboratory of Medical Analysis, Fujian Academy of Medical Sciences, Fuzhou 350001, ChinaShengli Clinical Medical College of Fujian Medical University, Fuzhou 350001, ChinaShengli Clinical Medical College of Fujian Medical University, Fuzhou 350001, ChinaFujian Key Laboratory of Medical Analysis, Fujian Academy of Medical Sciences, Fuzhou 350001, ChinaFujian Key Laboratory of Medical Analysis, Fujian Academy of Medical Sciences, Fuzhou 350001, ChinaFujian Key Laboratory of Medical Analysis, Fujian Academy of Medical Sciences, Fuzhou 350001, ChinaShengli Clinical Medical College of Fujian Medical University, Fuzhou 350001, ChinaShengli Clinical Medical College of Fujian Medical University, Fuzhou 350001, ChinaFujian Key Laboratory of Medical Analysis, Fujian Academy of Medical Sciences, Fuzhou 350001, China; Corresponding authors.Marfan syndrome (MFS) is a heritable dominant disorder of fibrous connective tissue, caused by mutations in the gene encoding fibrillin-1 on chromosome 15. Here, we report an induced pluripotent stem cell (iPSC) line generated from a patient with MFS who carries a heterozygous mutation of c.2777G > A(p.Cys926Tyr) in the FBN1 gene using an episomal method. The hiPS-MFS cell line has normal karyotype, expresses pluripotency markers, and has the ability to form three germ layers in vivo.This MFS-specific iPSC line can be used as a cell disease model to study the pathogenesis of Marfan syndrome.http://www.sciencedirect.com/science/article/pii/S1873506124002897
spellingShingle Ronghua Liu
Guoxing Weng
Fuzhen Zheng
Jinyan Chen
Kun Wang
Junyong Han
Jie Huang
Licheng Yan
Jingjun Jin
Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
Stem Cell Research
title Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
title_full Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
title_fullStr Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
title_full_unstemmed Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
title_short Generation of an integration-free induced pluripotent stem cell line, FJMAi001-A, from a Marfan syndrome patient with a heterozygous mutation c.2777G > A (p.Cys926Tyr) in FBN1
title_sort generation of an integration free induced pluripotent stem cell line fjmai001 a from a marfan syndrome patient with a heterozygous mutation c 2777g a p cys926tyr in fbn1
url http://www.sciencedirect.com/science/article/pii/S1873506124002897
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