Spectrum and risk of neoplasia in Werner syndrome: a systematic review.

<h4>Background</h4>Werner syndrome (WS) is an autosomal recessive genetic instability and progeroid ('premature aging') syndrome which is associated with an elevated risk of cancer.<h4>Objectives</h4>Our study objectives were to characterize the spectrum of neoplasi...

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Main Authors: Julia M Lauper, Alison Krause, Thomas L Vaughan, Raymond J Monnat
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2013-01-01
Series:PLoS ONE
Online Access:https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0059709&type=printable
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author Julia M Lauper
Alison Krause
Thomas L Vaughan
Raymond J Monnat
author_facet Julia M Lauper
Alison Krause
Thomas L Vaughan
Raymond J Monnat
author_sort Julia M Lauper
collection DOAJ
description <h4>Background</h4>Werner syndrome (WS) is an autosomal recessive genetic instability and progeroid ('premature aging') syndrome which is associated with an elevated risk of cancer.<h4>Objectives</h4>Our study objectives were to characterize the spectrum of neoplasia in WS using a well-documented study population, and to estimate the type-specific risk of neoplasia in WS relative to the general population.<h4>Methods</h4>We obtained case reports of neoplasms in WS patients through examining previous case series and reviews of WS, as well as through database searching in PubMed, Google Scholar, and J-EAST, a search engine for articles from Japan. We defined the spectrum (types and sites) of neoplasia in WS using all case reports, and were able to determine neoplasm type-specific risk in Japan WS patients by calculating standardized incidence and proportionate incidence ratios (SIR and SPIR, respectively) relative to Osaka Japan prefecture incidence rates.<h4>Results</h4>We used a newly assembled study population of 189 WS patients with 248 neoplasms to define the spectrum of neoplasia in WS. The most frequent neoplasms in WS patients, representing 2/3 of all reports, were thyroid neoplasms, malignant melanoma, meningioma, soft tissue sarcomas, leukemia and pre-leukemic conditions of the bone marrow, and primary bone neoplasms. Cancer risk defined by SIRs was significantly elevated in Japan-resident WS patients for the six most frequent neoplasms except leukemia, ranging from 53.5-fold for melanoma of the skin (95% CI: 24.5, 101.6) to 8.9 (95% CI: 4.9, 15.0) for thyroid neoplasms. Cancer risk as defined by SPIR was also significantly elevated for the most common malignancies except leukemia.<h4>Conclusions</h4>WS confers a strong predisposition to several specific types of neoplasia. These results serve as a guide for WS clinical care, and for additional analyses to define the mechanistic basis for cancer in WS and the general population.
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spelling doaj-art-67dc8b2aed6c4d2284095f7574e5ce6a2025-08-20T02:36:35ZengPublic Library of Science (PLoS)PLoS ONE1932-62032013-01-0184e5970910.1371/journal.pone.0059709Spectrum and risk of neoplasia in Werner syndrome: a systematic review.Julia M LauperAlison KrauseThomas L VaughanRaymond J Monnat<h4>Background</h4>Werner syndrome (WS) is an autosomal recessive genetic instability and progeroid ('premature aging') syndrome which is associated with an elevated risk of cancer.<h4>Objectives</h4>Our study objectives were to characterize the spectrum of neoplasia in WS using a well-documented study population, and to estimate the type-specific risk of neoplasia in WS relative to the general population.<h4>Methods</h4>We obtained case reports of neoplasms in WS patients through examining previous case series and reviews of WS, as well as through database searching in PubMed, Google Scholar, and J-EAST, a search engine for articles from Japan. We defined the spectrum (types and sites) of neoplasia in WS using all case reports, and were able to determine neoplasm type-specific risk in Japan WS patients by calculating standardized incidence and proportionate incidence ratios (SIR and SPIR, respectively) relative to Osaka Japan prefecture incidence rates.<h4>Results</h4>We used a newly assembled study population of 189 WS patients with 248 neoplasms to define the spectrum of neoplasia in WS. The most frequent neoplasms in WS patients, representing 2/3 of all reports, were thyroid neoplasms, malignant melanoma, meningioma, soft tissue sarcomas, leukemia and pre-leukemic conditions of the bone marrow, and primary bone neoplasms. Cancer risk defined by SIRs was significantly elevated in Japan-resident WS patients for the six most frequent neoplasms except leukemia, ranging from 53.5-fold for melanoma of the skin (95% CI: 24.5, 101.6) to 8.9 (95% CI: 4.9, 15.0) for thyroid neoplasms. Cancer risk as defined by SPIR was also significantly elevated for the most common malignancies except leukemia.<h4>Conclusions</h4>WS confers a strong predisposition to several specific types of neoplasia. These results serve as a guide for WS clinical care, and for additional analyses to define the mechanistic basis for cancer in WS and the general population.https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0059709&type=printable
spellingShingle Julia M Lauper
Alison Krause
Thomas L Vaughan
Raymond J Monnat
Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
PLoS ONE
title Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
title_full Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
title_fullStr Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
title_full_unstemmed Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
title_short Spectrum and risk of neoplasia in Werner syndrome: a systematic review.
title_sort spectrum and risk of neoplasia in werner syndrome a systematic review
url https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0059709&type=printable
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AT thomaslvaughan spectrumandriskofneoplasiainwernersyndromeasystematicreview
AT raymondjmonnat spectrumandriskofneoplasiainwernersyndromeasystematicreview