P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin
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| Main Authors: | , , , , , |
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| Format: | Article |
| Language: | English |
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Elsevier
2025-01-01
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| Series: | Genetics in Medicine Open |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774425009021 |
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| _version_ | 1849713295975514112 |
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| author | Jerry Vockley Shakuntala Basu Xue-Jun Zhao Bianca Seminotti Clinton Van't Land Al-Walid Mohsen |
| author_facet | Jerry Vockley Shakuntala Basu Xue-Jun Zhao Bianca Seminotti Clinton Van't Land Al-Walid Mohsen |
| author_sort | Jerry Vockley |
| collection | DOAJ |
| format | Article |
| id | doaj-art-61d6844f7ef44b41aef574d0070768a2 |
| institution | DOAJ |
| issn | 2949-7744 |
| language | English |
| publishDate | 2025-01-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Genetics in Medicine Open |
| spelling | doaj-art-61d6844f7ef44b41aef574d0070768a22025-08-20T03:14:00ZengElsevierGenetics in Medicine Open2949-77442025-01-01310286310.1016/j.gimo.2025.102863P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoinJerry Vockley0Shakuntala Basu1Xue-Jun Zhao2Bianca Seminotti3Clinton Van't Land4Al-Walid Mohsen5UPMC Children's Hospital of PittsburghUniversity of Pittsburgh School of MedicineUniversity of Pittsburgh School of MedicineUniversity of Pittsburgh School of MedicineUniversity of Pittsburgh School of MedicineUniversity of Pittsburgh School of Medicinehttp://www.sciencedirect.com/science/article/pii/S2949774425009021 |
| spellingShingle | Jerry Vockley Shakuntala Basu Xue-Jun Zhao Bianca Seminotti Clinton Van't Land Al-Walid Mohsen P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin Genetics in Medicine Open |
| title | P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin |
| title_full | P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin |
| title_fullStr | P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin |
| title_full_unstemmed | P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin |
| title_short | P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin |
| title_sort | p019 comparison of treatment efficacy of very long chain acyl coa vlcad deficiency with an aav9 hvlcad vector synthetic vlcad mrna and triheptanoin |
| url | http://www.sciencedirect.com/science/article/pii/S2949774425009021 |
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