Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up

Background. Mutations in the KCNJ11 gene, which encodes the Kir6.2 subunit of the ATP-sensitive potassium channel, often result in neonatal diabetes. Case. In this report, we describe a 10-year-old girl who is heterozygous for a new missense mutation in the KCNJ11 gene and whose treatm...

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Main Authors: Maja D Ješić, Helena Stock, Vera Zdravković, Smiljka Kovačević, Marko Savić, Miloš M Ješić
Format: Article
Language:English
Published: Hacettepe University Institute of Child Health 2021-06-01
Series:The Turkish Journal of Pediatrics
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Online Access:https://turkjpediatr.org/article/view/323
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author Maja D Ješić
Helena Stock
Vera Zdravković
Smiljka Kovačević
Marko Savić
Miloš M Ješić
author_facet Maja D Ješić
Helena Stock
Vera Zdravković
Smiljka Kovačević
Marko Savić
Miloš M Ješić
author_sort Maja D Ješić
collection DOAJ
description Background. Mutations in the KCNJ11 gene, which encodes the Kir6.2 subunit of the ATP-sensitive potassium channel, often result in neonatal diabetes. Case. In this report, we describe a 10-year-old girl who is heterozygous for a new missense mutation in the KCNJ11 gene and whose treatment was successfully switched from insulin to sulfonylurea (glibenclamide) therapy when she was one month old. 10-year data on a low-dose of glibenclamide monotherapy showed excellent glycaemic control with no reports of severe hypoglycaemia and microvascular complications. Conclusion. An early genetic diagnosis of neonatal diabetes mellitus is highly beneficial because early switch from insulin to sulfonylurea is safe, avoids unnecessary insulin therapy and promotes sustained improvement of glycaemic control on long-term follow-up.
format Article
id doaj-art-5b82db9ace3e49c8afdba5d086a550de
institution DOAJ
issn 0041-4301
2791-6421
language English
publishDate 2021-06-01
publisher Hacettepe University Institute of Child Health
record_format Article
series The Turkish Journal of Pediatrics
spelling doaj-art-5b82db9ace3e49c8afdba5d086a550de2025-08-20T02:55:41ZengHacettepe University Institute of Child HealthThe Turkish Journal of Pediatrics0041-43012791-64212021-06-0163310.24953/turkjped.2021.03.016Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-upMaja D JešićHelena Stock0Vera ZdravkovićSmiljka Kovačević1Marko Savić2Miloš M JešićDepartment of Pediatric Endocrinology, University Children's Hospital Tiršova, Belgrade.Department of Pediatric Endocrinology, University Children's Hospital Tiršova, Belgrade.Institute of Medical Statistics and Informatics, Faculty of Medicine, Belgrade, Serbia. Background. Mutations in the KCNJ11 gene, which encodes the Kir6.2 subunit of the ATP-sensitive potassium channel, often result in neonatal diabetes. Case. In this report, we describe a 10-year-old girl who is heterozygous for a new missense mutation in the KCNJ11 gene and whose treatment was successfully switched from insulin to sulfonylurea (glibenclamide) therapy when she was one month old. 10-year data on a low-dose of glibenclamide monotherapy showed excellent glycaemic control with no reports of severe hypoglycaemia and microvascular complications. Conclusion. An early genetic diagnosis of neonatal diabetes mellitus is highly beneficial because early switch from insulin to sulfonylurea is safe, avoids unnecessary insulin therapy and promotes sustained improvement of glycaemic control on long-term follow-up. https://turkjpediatr.org/article/view/323neonatal diabetes mellitusnew KCNJ11 mutationsulfonylurea therapy
spellingShingle Maja D Ješić
Helena Stock
Vera Zdravković
Smiljka Kovačević
Marko Savić
Miloš M Ješić
Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
The Turkish Journal of Pediatrics
neonatal diabetes mellitus
new KCNJ11 mutation
sulfonylurea therapy
title Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
title_full Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
title_fullStr Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
title_full_unstemmed Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
title_short Neonatal diabetes mellitus due to a new KCNJ11 mutation - 10 years of the patient`s follow-up
title_sort neonatal diabetes mellitus due to a new kcnj11 mutation 10 years of the patient s follow up
topic neonatal diabetes mellitus
new KCNJ11 mutation
sulfonylurea therapy
url https://turkjpediatr.org/article/view/323
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AT helenastock neonataldiabetesmellitusduetoanewkcnj11mutation10yearsofthepatientsfollowup
AT verazdravkovic neonataldiabetesmellitusduetoanewkcnj11mutation10yearsofthepatientsfollowup
AT smiljkakovacevic neonataldiabetesmellitusduetoanewkcnj11mutation10yearsofthepatientsfollowup
AT markosavic neonataldiabetesmellitusduetoanewkcnj11mutation10yearsofthepatientsfollowup
AT milosmjesic neonataldiabetesmellitusduetoanewkcnj11mutation10yearsofthepatientsfollowup