Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency

Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency

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Bibliographic Details
Main Authors:	Samia L. Pratt, Mariana Zarate-Mendez, Lidiia Koludarova, Sonja Jansson, Mikko Airavaara, Irena Hlushchuk, David Coleman, Caleb Heffner, Rita Horvath, Brendan J. Battersby, Robert W. Burgess
Format:	Article
Language:	English
Published:	The Company of Biologists 2025-05-01
Series:	Disease Models & Mechanisms
Subjects:	c12orf65 leigh syndrome cmt6 mitochondrial translation mrpl58 behr's syndrome
Online Access:	http://dmm.biologists.org/content/18/5/dmm052120
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