Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation

The HBB gene encodes the β-globin protein, one of the two main components of adult hemoglobin A (HbA) responsible for oxygen transport. β-thalassemia is a genetic disorder caused by mutations affecting β-globin chain synthesis, leading to reduced or absent β-globin production, impaired erythropoiesi...

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Main Authors: Pawarit Innachai, Gunn Pornratananont, Chonthicha Satirapod, Usanarat Anurathapan, Duantida Songdej, Amornrat Tangprasittipap, Suradej Hongeng
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Stem Cell Research
Online Access:http://www.sciencedirect.com/science/article/pii/S1873506125000522
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author Pawarit Innachai
Gunn Pornratananont
Chonthicha Satirapod
Usanarat Anurathapan
Duantida Songdej
Amornrat Tangprasittipap
Suradej Hongeng
author_facet Pawarit Innachai
Gunn Pornratananont
Chonthicha Satirapod
Usanarat Anurathapan
Duantida Songdej
Amornrat Tangprasittipap
Suradej Hongeng
author_sort Pawarit Innachai
collection DOAJ
description The HBB gene encodes the β-globin protein, one of the two main components of adult hemoglobin A (HbA) responsible for oxygen transport. β-thalassemia is a genetic disorder caused by mutations affecting β-globin chain synthesis, leading to reduced or absent β-globin production, impaired erythropoiesis, and generally results in anemia. In this study, the human-induced pluripotent stem cell line (hiPSC) MURAi006-A was generated from male fetal skin fibroblasts carrying both a β⁰-thalassemia mutation at codon 17 (A > T) and a codon 26 (G > A) HbE mutation using non-integrative reprogramming episomes.
format Article
id doaj-art-570e36da5b1c4352bbaabe3797da64db
institution DOAJ
issn 1873-5061
language English
publishDate 2025-06-01
publisher Elsevier
record_format Article
series Stem Cell Research
spelling doaj-art-570e36da5b1c4352bbaabe3797da64db2025-08-20T03:14:45ZengElsevierStem Cell Research1873-50612025-06-018510370210.1016/j.scr.2025.103702Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutationPawarit Innachai0Gunn Pornratananont1Chonthicha Satirapod2Usanarat Anurathapan3Duantida Songdej4Amornrat Tangprasittipap5Suradej Hongeng6Offices of Health Science Research, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, ThailandProgram in Translational Medicine, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, ThailandDepartment of Obstetrics and Gynecology, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, ThailandDepartment of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, ThailandDepartment of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, ThailandOffices of Health Science Research, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, Thailand; Corresponding author.Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, ThailandThe HBB gene encodes the β-globin protein, one of the two main components of adult hemoglobin A (HbA) responsible for oxygen transport. β-thalassemia is a genetic disorder caused by mutations affecting β-globin chain synthesis, leading to reduced or absent β-globin production, impaired erythropoiesis, and generally results in anemia. In this study, the human-induced pluripotent stem cell line (hiPSC) MURAi006-A was generated from male fetal skin fibroblasts carrying both a β⁰-thalassemia mutation at codon 17 (A > T) and a codon 26 (G > A) HbE mutation using non-integrative reprogramming episomes.http://www.sciencedirect.com/science/article/pii/S1873506125000522
spellingShingle Pawarit Innachai
Gunn Pornratananont
Chonthicha Satirapod
Usanarat Anurathapan
Duantida Songdej
Amornrat Tangprasittipap
Suradej Hongeng
Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
Stem Cell Research
title Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
title_full Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
title_fullStr Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
title_full_unstemmed Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
title_short Generation of an integration-free induced pluripotent stem cell line, MURAi006-A, from a hemoglobin E/β-thalassemia patient harboring the βE/β0 (Codon 17, A > T) compound heterozygous mutation
title_sort generation of an integration free induced pluripotent stem cell line murai006 a from a hemoglobin e β thalassemia patient harboring the βe β0 codon 17 a t compound heterozygous mutation
url http://www.sciencedirect.com/science/article/pii/S1873506125000522
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