Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker

Abstract A significant challenge for chimeric antigen receptor (CAR) T cell therapy against glioblastoma (GBM) is its immunosuppressive microenvironment, which is densely populated by protumoral glioma-associated microglia and macrophages (GAMs). Myeloid immune checkpoint therapy targeting the CD47-...

Full description

Saved in:
Bibliographic Details
Main Authors: Tomás A. Martins, Deniz Kaymak, Nazanin Tatari, Fiona Gerster, Sabrina Hogan, Marie-Françoise Ritz, Valerio Sabatino, Ronja Wieboldt, Ewelina M. Bartoszek, Marta McDaid, Alexandra Gerber, Alicia Buck, Aisha Beshirova, Anja Heider, Tala Shekarian, Hayget Mohamed, Manina M. Etter, Philip Schmassmann, Ines Abel, Jean-Louis Boulay, Yasuyuki Saito, Luigi Mariani, Raphael Guzman, Berend Snijder, Tobias Weiss, Heinz Läubli, Gregor Hutter
Format: Article
Language:English
Published: Nature Portfolio 2024-11-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-024-54129-w
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850061749282144256
author Tomás A. Martins
Deniz Kaymak
Nazanin Tatari
Fiona Gerster
Sabrina Hogan
Marie-Françoise Ritz
Valerio Sabatino
Ronja Wieboldt
Ewelina M. Bartoszek
Marta McDaid
Alexandra Gerber
Alicia Buck
Aisha Beshirova
Anja Heider
Tala Shekarian
Hayget Mohamed
Manina M. Etter
Philip Schmassmann
Ines Abel
Jean-Louis Boulay
Yasuyuki Saito
Luigi Mariani
Raphael Guzman
Berend Snijder
Tobias Weiss
Heinz Läubli
Gregor Hutter
author_facet Tomás A. Martins
Deniz Kaymak
Nazanin Tatari
Fiona Gerster
Sabrina Hogan
Marie-Françoise Ritz
Valerio Sabatino
Ronja Wieboldt
Ewelina M. Bartoszek
Marta McDaid
Alexandra Gerber
Alicia Buck
Aisha Beshirova
Anja Heider
Tala Shekarian
Hayget Mohamed
Manina M. Etter
Philip Schmassmann
Ines Abel
Jean-Louis Boulay
Yasuyuki Saito
Luigi Mariani
Raphael Guzman
Berend Snijder
Tobias Weiss
Heinz Läubli
Gregor Hutter
author_sort Tomás A. Martins
collection DOAJ
description Abstract A significant challenge for chimeric antigen receptor (CAR) T cell therapy against glioblastoma (GBM) is its immunosuppressive microenvironment, which is densely populated by protumoral glioma-associated microglia and macrophages (GAMs). Myeloid immune checkpoint therapy targeting the CD47-signal regulatory protein alpha (SIRPα) axis induces GAM phagocytic function, but CD47 blockade monotherapy is associated with toxicity and low bioavailability in solid tumors. In this work, we engineer a CAR T cell against epidermal growth factor receptor variant III (EGFRvIII), constitutively secreting a signal regulatory protein gamma-related protein (SGRP) with high affinity to CD47. Anti-EGFRvIII-SGRP CAR T cells eradicate orthotopic EGFRvIII-mosaic GBM in vivo, promoting GAM-mediated tumor cell phagocytosis. In a subcutaneous CD19+ lymphoma mouse model, anti-CD19-SGRP CAR T cell therapy is superior to conventional anti-CD19 CAR T. Thus, combination of CAR and SGRP eliminates bystander tumor cells in a manner that could overcome main mechanisms of CAR T cell therapy resistance, including immune suppression and antigen escape.
format Article
id doaj-art-54d8c2ce535347fc8b97105d49f0cbda
institution DOAJ
issn 2041-1723
language English
publishDate 2024-11-01
publisher Nature Portfolio
record_format Article
series Nature Communications
spelling doaj-art-54d8c2ce535347fc8b97105d49f0cbda2025-08-20T02:50:08ZengNature PortfolioNature Communications2041-17232024-11-0115112510.1038/s41467-024-54129-wEnhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blockerTomás A. Martins0Deniz Kaymak1Nazanin Tatari2Fiona Gerster3Sabrina Hogan4Marie-Françoise Ritz5Valerio Sabatino6Ronja Wieboldt7Ewelina M. Bartoszek8Marta McDaid9Alexandra Gerber10Alicia Buck11Aisha Beshirova12Anja Heider13Tala Shekarian14Hayget Mohamed15Manina M. Etter16Philip Schmassmann17Ines Abel18Jean-Louis Boulay19Yasuyuki Saito20Luigi Mariani21Raphael Guzman22Berend Snijder23Tobias Weiss24Heinz Läubli25Gregor Hutter26Brain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselCancer Immunotherapy, Department of Biomedicine, University of BaselMicroscopy Core Facility, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselInstitute of Molecular Systems Biology, ETH ZurichExperimental Immunology, Department of Biomedicine, University of BaselSwiss Institute of Allergy and Asthma Research, University of ZurichBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselDepartment of Neurosurgery, University Hospital BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselDivision of Molecular and Cellular Signaling, Department of Biochemistry and Molecular Biology, Kobe University Graduate School of MedicineDepartment of Neurosurgery, University Hospital BaselDepartment of Neurosurgery, University Hospital BaselInstitute of Molecular Systems Biology, ETH ZurichDepartment of Neurology, Clinical Neuroscience Center, University Hospital ZurichCancer Immunotherapy, Department of Biomedicine, University of BaselBrain Tumor Immunotherapy and Biology, Department of Biomedicine, University of BaselAbstract A significant challenge for chimeric antigen receptor (CAR) T cell therapy against glioblastoma (GBM) is its immunosuppressive microenvironment, which is densely populated by protumoral glioma-associated microglia and macrophages (GAMs). Myeloid immune checkpoint therapy targeting the CD47-signal regulatory protein alpha (SIRPα) axis induces GAM phagocytic function, but CD47 blockade monotherapy is associated with toxicity and low bioavailability in solid tumors. In this work, we engineer a CAR T cell against epidermal growth factor receptor variant III (EGFRvIII), constitutively secreting a signal regulatory protein gamma-related protein (SGRP) with high affinity to CD47. Anti-EGFRvIII-SGRP CAR T cells eradicate orthotopic EGFRvIII-mosaic GBM in vivo, promoting GAM-mediated tumor cell phagocytosis. In a subcutaneous CD19+ lymphoma mouse model, anti-CD19-SGRP CAR T cell therapy is superior to conventional anti-CD19 CAR T. Thus, combination of CAR and SGRP eliminates bystander tumor cells in a manner that could overcome main mechanisms of CAR T cell therapy resistance, including immune suppression and antigen escape.https://doi.org/10.1038/s41467-024-54129-w
spellingShingle Tomás A. Martins
Deniz Kaymak
Nazanin Tatari
Fiona Gerster
Sabrina Hogan
Marie-Françoise Ritz
Valerio Sabatino
Ronja Wieboldt
Ewelina M. Bartoszek
Marta McDaid
Alexandra Gerber
Alicia Buck
Aisha Beshirova
Anja Heider
Tala Shekarian
Hayget Mohamed
Manina M. Etter
Philip Schmassmann
Ines Abel
Jean-Louis Boulay
Yasuyuki Saito
Luigi Mariani
Raphael Guzman
Berend Snijder
Tobias Weiss
Heinz Läubli
Gregor Hutter
Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
Nature Communications
title Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
title_full Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
title_fullStr Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
title_full_unstemmed Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
title_short Enhancing anti-EGFRvIII CAR T cell therapy against glioblastoma with a paracrine SIRPγ-derived CD47 blocker
title_sort enhancing anti egfrviii car t cell therapy against glioblastoma with a paracrine sirpγ derived cd47 blocker
url https://doi.org/10.1038/s41467-024-54129-w
work_keys_str_mv AT tomasamartins enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT denizkaymak enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT nazanintatari enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT fionagerster enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT sabrinahogan enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT mariefrancoiseritz enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT valeriosabatino enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT ronjawieboldt enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT ewelinambartoszek enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT martamcdaid enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT alexandragerber enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT aliciabuck enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT aishabeshirova enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT anjaheider enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT talashekarian enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT haygetmohamed enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT maninametter enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT philipschmassmann enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT inesabel enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT jeanlouisboulay enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT yasuyukisaito enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT luigimariani enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT raphaelguzman enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT berendsnijder enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT tobiasweiss enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT heinzlaubli enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker
AT gregorhutter enhancingantiegfrviiicartcelltherapyagainstglioblastomawithaparacrinesirpgderivedcd47blocker