The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region

mAbs play an essential role in the therapeutic arsenal. Our laboratory has patented the Rendomab-B49 mAb targeting the endothelin B receptor (ETB). This G protein-coupled receptor plays a driving role in the progression of numerous cancers. We chimerized our mAb (xiRB49) to evaluate its preclinical...

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Main Authors: Marie Hautiere, Irene Maffucci, Narciso Costa, Amaury Herbet, Sosthene Essono, Séverine Padiolleau-Lefevre, Didier Boquet
Format: Article
Language:English
Published: Taylor & Francis Group 2023-12-01
Series:Human Vaccines & Immunotherapeutics
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Online Access:https://www.tandfonline.com/doi/10.1080/21645515.2023.2279867
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author Marie Hautiere
Irene Maffucci
Narciso Costa
Amaury Herbet
Sosthene Essono
Séverine Padiolleau-Lefevre
Didier Boquet
author_facet Marie Hautiere
Irene Maffucci
Narciso Costa
Amaury Herbet
Sosthene Essono
Séverine Padiolleau-Lefevre
Didier Boquet
author_sort Marie Hautiere
collection DOAJ
description mAbs play an essential role in the therapeutic arsenal. Our laboratory has patented the Rendomab-B49 mAb targeting the endothelin B receptor (ETB). This G protein-coupled receptor plays a driving role in the progression of numerous cancers. We chimerized our mAb (xiRB49) to evaluate its preclinical therapeutic efficacy in different ETB+ tumor models with an antibody drug conjugate approach. As previously reported, the chimerization process of an antibody can alter its functionality. In this article, we present the chimerization of RB49. xiRB49 purified by Protein A remained perfectly soluble and did not aggregate, but it lost all its ability to recognize ETB. A detailed analysis of its variable region using IMGT tools allowed us to identify an unusual proline at position 125. In silico mAb modeling and in vitro experiments were performed for a better understanding of xiRB49 structure-function relationships. Our results show that the proline in position 125 on the heavy chain alters the xiRB49 CDR3 light chain conformation and its mutation to threonine allows complete functional recovery.
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publishDate 2023-12-01
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series Human Vaccines & Immunotherapeutics
spelling doaj-art-5457d5c48a09474cae6ab11171ce34f82025-08-20T03:26:39ZengTaylor & Francis GroupHuman Vaccines & Immunotherapeutics2164-55152164-554X2023-12-0119310.1080/21645515.2023.2279867The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable regionMarie Hautiere0Irene Maffucci1Narciso Costa2Amaury Herbet3Sosthene Essono4Séverine Padiolleau-Lefevre5Didier Boquet6Département Médicaments et Technologies pour la Santé (DMTS), SPI, Université Paris-Saclay, CEA, Gif-sur-Yvette, FranceCentre de Recherche de Royallieu, CNRS UMR 7025, Génie Enzymatique et Cellulaire, Compiègne Cedex, FranceDépartement Médicaments et Technologies pour la Santé (DMTS), SPI, Université Paris-Saclay, CEA, Gif-sur-Yvette, FranceDépartement Médicaments et Technologies pour la Santé (DMTS), SPI, Université Paris-Saclay, CEA, Gif-sur-Yvette, FranceMedical Biotechnology Engineering LLC, Malden, MA, USACentre de Recherche de Royallieu, CNRS UMR 7025, Génie Enzymatique et Cellulaire, Compiègne Cedex, FranceDépartement Médicaments et Technologies pour la Santé (DMTS), SPI, Université Paris-Saclay, CEA, Gif-sur-Yvette, FrancemAbs play an essential role in the therapeutic arsenal. Our laboratory has patented the Rendomab-B49 mAb targeting the endothelin B receptor (ETB). This G protein-coupled receptor plays a driving role in the progression of numerous cancers. We chimerized our mAb (xiRB49) to evaluate its preclinical therapeutic efficacy in different ETB+ tumor models with an antibody drug conjugate approach. As previously reported, the chimerization process of an antibody can alter its functionality. In this article, we present the chimerization of RB49. xiRB49 purified by Protein A remained perfectly soluble and did not aggregate, but it lost all its ability to recognize ETB. A detailed analysis of its variable region using IMGT tools allowed us to identify an unusual proline at position 125. In silico mAb modeling and in vitro experiments were performed for a better understanding of xiRB49 structure-function relationships. Our results show that the proline in position 125 on the heavy chain alters the xiRB49 CDR3 light chain conformation and its mutation to threonine allows complete functional recovery.https://www.tandfonline.com/doi/10.1080/21645515.2023.2279867Monoclonal antibodychimerizationprolinein silico modelling
spellingShingle Marie Hautiere
Irene Maffucci
Narciso Costa
Amaury Herbet
Sosthene Essono
Séverine Padiolleau-Lefevre
Didier Boquet
The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
Human Vaccines & Immunotherapeutics
Monoclonal antibody
chimerization
proline
in silico modelling
title The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
title_full The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
title_fullStr The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
title_full_unstemmed The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
title_short The functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
title_sort functionality of a therapeutic antibody candidate restored by a single mutation from proline to threonine in the variable region
topic Monoclonal antibody
chimerization
proline
in silico modelling
url https://www.tandfonline.com/doi/10.1080/21645515.2023.2279867
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