VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300

Studies on Hippo pathway regulation of tumorigenesis largely center on YAP and TAZ, the transcriptional co-regulators of TEADs. Here, we present an oncogenic mechanism involving VGLL and TEAD fusions that is Hippo pathway-related but YAP/TAZ-independent. We characterize two recurrent fusions, VGLL2-...

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Main Authors: Susu Guo, Xiaodi Hu, Jennifer L Cotton, Lifang Ma, Qi Li, Jiangtao Cui, Yongjie Wang, Ritesh P Thakare, Zhipeng Tao, Y Tony Ip, Xu Wu, Jiayi Wang, Junhao Mao
Format: Article
Language:English
Published: eLife Sciences Publications Ltd 2025-05-01
Series:eLife
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Online Access:https://elifesciences.org/articles/98386
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author Susu Guo
Xiaodi Hu
Jennifer L Cotton
Lifang Ma
Qi Li
Jiangtao Cui
Yongjie Wang
Ritesh P Thakare
Zhipeng Tao
Y Tony Ip
Xu Wu
Jiayi Wang
Junhao Mao
author_facet Susu Guo
Xiaodi Hu
Jennifer L Cotton
Lifang Ma
Qi Li
Jiangtao Cui
Yongjie Wang
Ritesh P Thakare
Zhipeng Tao
Y Tony Ip
Xu Wu
Jiayi Wang
Junhao Mao
author_sort Susu Guo
collection DOAJ
description Studies on Hippo pathway regulation of tumorigenesis largely center on YAP and TAZ, the transcriptional co-regulators of TEADs. Here, we present an oncogenic mechanism involving VGLL and TEAD fusions that is Hippo pathway-related but YAP/TAZ-independent. We characterize two recurrent fusions, VGLL2-NCOA2 and TEAD1-NCOA2, recently identified in human spindle cell rhabdomyosarcoma. We demonstrate that in contrast to VGLL2 and TEAD1 the fusion proteins are potent activators of TEAD-dependent transcription, and the function of these fusion proteins does not require YAP/TAZ. Furthermore, we identify that VGLL2 and TEAD1 fusions engage specific epigenetic regulation by recruiting histone acetyltransferase EP300 to control TEAD-mediated transcriptional and epigenetic landscapes. We show that small-molecule EP300 inhibition can suppress fusion protein-induced oncogenic transformation both in vitro and in vivo in mouse models. Overall, our study reveals a molecular basis for VGLL involvement in cancer and provides a framework for targeting tumors carrying VGLL, TEAD, or NCOA translocations.
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spelling doaj-art-5337db03441e40b8a9611a3f6f6368842025-08-20T02:14:23ZengeLife Sciences Publications LtdeLife2050-084X2025-05-011310.7554/eLife.98386VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300Susu Guo0https://orcid.org/0000-0002-7481-6884Xiaodi Hu1Jennifer L Cotton2https://orcid.org/0000-0003-0106-1801Lifang Ma3Qi Li4Jiangtao Cui5Yongjie Wang6Ritesh P Thakare7Zhipeng Tao8Y Tony Ip9https://orcid.org/0000-0003-4370-7906Xu Wu10Jiayi Wang11https://orcid.org/0000-0003-1688-2864Junhao Mao12https://orcid.org/0000-0003-1980-1177Department of Clinical Laboratory, Shanghai Chest Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, ChinaDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, United StatesDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, United StatesDepartment of Clinical Laboratory, Shanghai Chest Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, ChinaDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, United States; Program in Molecular Medicine, University of Massachusetts Chan Medical School, Worcester, United StatesDepartment of Clinical Laboratory, Shanghai Chest Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, ChinaDepartment of Clinical Laboratory, Shanghai Chest Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, ChinaDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, United StatesCutaneous Biology Research Center, Massachusetts General Hospital, Harvard Medical School, Charlestown, United StatesProgram in Molecular Medicine, University of Massachusetts Chan Medical School, Worcester, United StatesCutaneous Biology Research Center, Massachusetts General Hospital, Harvard Medical School, Charlestown, United StatesDepartment of Clinical Laboratory, Shanghai Chest Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, ChinaDepartment of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, United StatesStudies on Hippo pathway regulation of tumorigenesis largely center on YAP and TAZ, the transcriptional co-regulators of TEADs. Here, we present an oncogenic mechanism involving VGLL and TEAD fusions that is Hippo pathway-related but YAP/TAZ-independent. We characterize two recurrent fusions, VGLL2-NCOA2 and TEAD1-NCOA2, recently identified in human spindle cell rhabdomyosarcoma. We demonstrate that in contrast to VGLL2 and TEAD1 the fusion proteins are potent activators of TEAD-dependent transcription, and the function of these fusion proteins does not require YAP/TAZ. Furthermore, we identify that VGLL2 and TEAD1 fusions engage specific epigenetic regulation by recruiting histone acetyltransferase EP300 to control TEAD-mediated transcriptional and epigenetic landscapes. We show that small-molecule EP300 inhibition can suppress fusion protein-induced oncogenic transformation both in vitro and in vivo in mouse models. Overall, our study reveals a molecular basis for VGLL involvement in cancer and provides a framework for targeting tumors carrying VGLL, TEAD, or NCOA translocations.https://elifesciences.org/articles/98386VGLL2TEADHIPPOYAPNCOA2EP300
spellingShingle Susu Guo
Xiaodi Hu
Jennifer L Cotton
Lifang Ma
Qi Li
Jiangtao Cui
Yongjie Wang
Ritesh P Thakare
Zhipeng Tao
Y Tony Ip
Xu Wu
Jiayi Wang
Junhao Mao
VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
eLife
VGLL2
TEAD
HIPPO
YAP
NCOA2
EP300
title VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
title_full VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
title_fullStr VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
title_full_unstemmed VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
title_short VGLL2 and TEAD1 fusion proteins identified in human sarcoma drive YAP/TAZ-independent tumorigenesis by engaging EP300
title_sort vgll2 and tead1 fusion proteins identified in human sarcoma drive yap taz independent tumorigenesis by engaging ep300
topic VGLL2
TEAD
HIPPO
YAP
NCOA2
EP300
url https://elifesciences.org/articles/98386
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