Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement

Nanotheranostics—where nanoscale materials serve both diagnostic and therapeutic functions—are rapidly transforming gene therapy by tackling critical delivery challenges. This review explores the design and engineering of various nanoparticle systems (lipid-based, polymeric, inorganic, and hybrid) t...

Full description

Saved in:
Bibliographic Details
Main Authors: Paula Guzmán-Sastoque, Cristian F. Rodríguez, María Camila Monsalve, Stiven Castellanos, Andrés Manrique-Moreno, Luis H. Reyes, Juan C. Cruz
Format: Article
Language:English
Published: MDPI AG 2025-04-01
Series:Journal of Nanotheranostics
Subjects:
Online Access:https://www.mdpi.com/2624-845X/6/2/10
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849705823302844416
author Paula Guzmán-Sastoque
Cristian F. Rodríguez
María Camila Monsalve
Stiven Castellanos
Andrés Manrique-Moreno
Luis H. Reyes
Juan C. Cruz
author_facet Paula Guzmán-Sastoque
Cristian F. Rodríguez
María Camila Monsalve
Stiven Castellanos
Andrés Manrique-Moreno
Luis H. Reyes
Juan C. Cruz
author_sort Paula Guzmán-Sastoque
collection DOAJ
description Nanotheranostics—where nanoscale materials serve both diagnostic and therapeutic functions—are rapidly transforming gene therapy by tackling critical delivery challenges. This review explores the design and engineering of various nanoparticle systems (lipid-based, polymeric, inorganic, and hybrid) to enhance stability, targeting, and endosomal escape of genetic payloads. We discuss how real-time imaging capabilities integrated into these platforms enable precise localization and controlled release of genes, improving treatment efficacy while reducing off-target effects. Key strategies to overcome delivery barriers (such as proton sponge effect and photothermal disruption) and to achieve nuclear localization are highlighted, along with recent advances in stimuli-responsive systems that facilitate spatiotemporal control of gene expression. Clinical trials and preclinical studies demonstrate the expanding role of nanotheranostics in managing cancer, inherited disorders, and cardiovascular and neurological diseases. We further address regulatory and manufacturing hurdles that must be overcome for the widespread clinical adoption of nanoparticle-based gene therapies. By synthesizing recent progress and ongoing challenges, this review underscores the transformative potential of nanotheranostics for effective, targeted, and image-guided gene delivery.
format Article
id doaj-art-4d48252641d84a7ca479fd41b65bb1c3
institution DOAJ
issn 2624-845X
language English
publishDate 2025-04-01
publisher MDPI AG
record_format Article
series Journal of Nanotheranostics
spelling doaj-art-4d48252641d84a7ca479fd41b65bb1c32025-08-20T03:16:22ZengMDPI AGJournal of Nanotheranostics2624-845X2025-04-01621010.3390/jnt6020010Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery EnhancementPaula Guzmán-Sastoque0Cristian F. Rodríguez1María Camila Monsalve2Stiven Castellanos3Andrés Manrique-Moreno4Luis H. Reyes5Juan C. Cruz6Biomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaBiomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaBiomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaBiomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaBiomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaGrupo de Diseño de Productos y Procesos (GDPP), Department of Chemical and Food Engineering, Universidad de los Andes, Bogotá 111711, ColombiaBiomedical Engineering Department, Universidad de los Andes, Bogotá 111711, ColombiaNanotheranostics—where nanoscale materials serve both diagnostic and therapeutic functions—are rapidly transforming gene therapy by tackling critical delivery challenges. This review explores the design and engineering of various nanoparticle systems (lipid-based, polymeric, inorganic, and hybrid) to enhance stability, targeting, and endosomal escape of genetic payloads. We discuss how real-time imaging capabilities integrated into these platforms enable precise localization and controlled release of genes, improving treatment efficacy while reducing off-target effects. Key strategies to overcome delivery barriers (such as proton sponge effect and photothermal disruption) and to achieve nuclear localization are highlighted, along with recent advances in stimuli-responsive systems that facilitate spatiotemporal control of gene expression. Clinical trials and preclinical studies demonstrate the expanding role of nanotheranostics in managing cancer, inherited disorders, and cardiovascular and neurological diseases. We further address regulatory and manufacturing hurdles that must be overcome for the widespread clinical adoption of nanoparticle-based gene therapies. By synthesizing recent progress and ongoing challenges, this review underscores the transformative potential of nanotheranostics for effective, targeted, and image-guided gene delivery.https://www.mdpi.com/2624-845X/6/2/10nanotheranosticsstimuli-responsive nanoparticlesendosomal escapetargeted gene deliveryCRISPR/Cas gene editing
spellingShingle Paula Guzmán-Sastoque
Cristian F. Rodríguez
María Camila Monsalve
Stiven Castellanos
Andrés Manrique-Moreno
Luis H. Reyes
Juan C. Cruz
Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
Journal of Nanotheranostics
nanotheranostics
stimuli-responsive nanoparticles
endosomal escape
targeted gene delivery
CRISPR/Cas gene editing
title Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
title_full Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
title_fullStr Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
title_full_unstemmed Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
title_short Nanotheranostics Revolutionizing Gene Therapy: Emerging Applications in Gene Delivery Enhancement
title_sort nanotheranostics revolutionizing gene therapy emerging applications in gene delivery enhancement
topic nanotheranostics
stimuli-responsive nanoparticles
endosomal escape
targeted gene delivery
CRISPR/Cas gene editing
url https://www.mdpi.com/2624-845X/6/2/10
work_keys_str_mv AT paulaguzmansastoque nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT cristianfrodriguez nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT mariacamilamonsalve nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT stivencastellanos nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT andresmanriquemoreno nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT luishreyes nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement
AT juanccruz nanotheranosticsrevolutionizinggenetherapyemergingapplicationsingenedeliveryenhancement