Rational design of lipid nanoparticles for enabling gene therapies
Lipid nanoparticle (LNP) technology is increasingly enabling RNA-based gene therapies that can potentially be used to treat most diseases. Further, these LNP RNA therapeutics can be designed and manufactured in a matter of weeks, allowing personalized medicines that can be produced in a time frame r...
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| Main Authors: | Cedric A. Brimacombe, Jayesh A. Kulkarni, Miffy H.Y. Cheng, Kevin An, Dominik Witzigmann, Pieter R. Cullis |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2025-09-01
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| Series: | Molecular Therapy: Methods & Clinical Development |
| Subjects: | |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2329050125001135 |
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