Quality of Life with Late-Onset Pompe Disease: Qualitative Interviews and General Public Utility Estimation in the United Kingdom
**Background:** Late-onset Pompe disease (LOPD) is a rare, progressive neuromuscular condition typically characterized by weakness of skeletal muscles, including those involved in respiration and diaphragmatic dysfunction. Individuals with LOPD typically eventually require mobility and/or ventilator...
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Main Authors: | Lena Hubig, Anna-Katrine Sussex, Alasdair MacCulloch, Derralynn Hughes, Ryan Graham, Liz Morris, Syed Raza, Andrew J. Lloyd, Amanda Sowinski, Katy Gallop |
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Format: | Article |
Language: | English |
Published: |
Columbia Data Analytics, LLC
2023-03-01
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Series: | Journal of Health Economics and Outcomes Research |
Online Access: | https://doi.org/10.36469/001c.68157 |
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