Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes

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Main Authors: Hiroyuki Chaya, Mitsuru Naito, Kazuko Toh, Naoki Yamada, Kaori Taniwaki, Yurugi Kinoshita, Shigeto Fukushima, Katsura Minegishi, Yoshitsugu Aoki, Tetsuya Nagata, Takanori Yokota, Kazunori Kataoka, Kanjiro Miyata
Format: Article
Language:English
Published: American Chemical Society 2025-08-01
Series:ACS Omega
Online Access:https://doi.org/10.1021/acsomega.5c02207
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author Hiroyuki Chaya
Mitsuru Naito
Kazuko Toh
Naoki Yamada
Kaori Taniwaki
Yurugi Kinoshita
Shigeto Fukushima
Katsura Minegishi
Yoshitsugu Aoki
Tetsuya Nagata
Takanori Yokota
Kazunori Kataoka
Kanjiro Miyata
author_facet Hiroyuki Chaya
Mitsuru Naito
Kazuko Toh
Naoki Yamada
Kaori Taniwaki
Yurugi Kinoshita
Shigeto Fukushima
Katsura Minegishi
Yoshitsugu Aoki
Tetsuya Nagata
Takanori Yokota
Kazunori Kataoka
Kanjiro Miyata
author_sort Hiroyuki Chaya
collection DOAJ
format Article
id doaj-art-485013e020ce44ebbbad109d16626328
institution Kabale University
issn 2470-1343
language English
publishDate 2025-08-01
publisher American Chemical Society
record_format Article
series ACS Omega
spelling doaj-art-485013e020ce44ebbbad109d166263282025-08-20T03:36:07ZengAmerican Chemical SocietyACS Omega2470-13432025-08-011031343633437110.1021/acsomega.5c02207Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion ComplexesHiroyuki Chaya0Mitsuru Naito1Kazuko Toh2Naoki Yamada3Kaori Taniwaki4Yurugi Kinoshita5Shigeto Fukushima6Katsura Minegishi7Yoshitsugu Aoki8Tetsuya Nagata9Takanori Yokota10Kazunori Kataoka11Kanjiro Miyata12Department of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, JapanDepartment of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, JapanInnovation Center of NanoMedicine, Kawasaki Institute of Industrial Promotion, Kawasaki, JapanDepartment of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, JapanDepartment of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, JapanDepartment of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, JapanInnovation Center of NanoMedicine, Kawasaki Institute of Industrial Promotion, Kawasaki, JapanDepartment of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Tokyo, JapanDepartment of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Tokyo, JapanDepartment of Neurology and Neurological Science, Graduate School of Medical and Dental Science, Tokyo Medical and Dental University, Tokyo, JapanDepartment of Neurology and Neurological Science, Graduate School of Medical and Dental Science, Tokyo Medical and Dental University, Tokyo, JapanInnovation Center of NanoMedicine, Kawasaki Institute of Industrial Promotion, Kawasaki, JapanDepartment of Materials Engineering, Graduate School of Engineering, The University of Tokyo, Tokyo, Japanhttps://doi.org/10.1021/acsomega.5c02207
spellingShingle Hiroyuki Chaya
Mitsuru Naito
Kazuko Toh
Naoki Yamada
Kaori Taniwaki
Yurugi Kinoshita
Shigeto Fukushima
Katsura Minegishi
Yoshitsugu Aoki
Tetsuya Nagata
Takanori Yokota
Kazunori Kataoka
Kanjiro Miyata
Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
ACS Omega
title Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
title_full Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
title_fullStr Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
title_full_unstemmed Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
title_short Enhanced Accumulation of Heteroduplex Oligonucleotides in Dystrophin-Deficient Skeletal Muscles by Single Oligonucleotide-Loaded Unit Polyion Complexes
title_sort enhanced accumulation of heteroduplex oligonucleotides in dystrophin deficient skeletal muscles by single oligonucleotide loaded unit polyion complexes
url https://doi.org/10.1021/acsomega.5c02207
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