Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis
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| Main Authors: | , , , , |
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| Format: | Article |
| Language: | English |
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Elsevier
2025-09-01
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| Series: | JHEP Reports |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2589555925001648 |
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| author | Claudia Mandato Mario Masarone Mariano Festa Pietro Torre Marcello Persico |
| author_facet | Claudia Mandato Mario Masarone Mariano Festa Pietro Torre Marcello Persico |
| author_sort | Claudia Mandato |
| collection | DOAJ |
| format | Article |
| id | doaj-art-47be32bb76f847c78baed5fd87c3f1fe |
| institution | Kabale University |
| issn | 2589-5559 |
| language | English |
| publishDate | 2025-09-01 |
| publisher | Elsevier |
| record_format | Article |
| series | JHEP Reports |
| spelling | doaj-art-47be32bb76f847c78baed5fd87c3f1fe2025-08-20T03:59:37ZengElsevierJHEP Reports2589-55592025-09-017910148610.1016/j.jhepr.2025.101486Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosisClaudia Mandato0Mario Masarone1Mariano Festa2Pietro Torre3Marcello Persico4Pediatric Hepatology, Department of Medicine, Surgery and Dentistry “Scuola Medica Salernitana”, Pediatrics Section, University of Salerno, Baronissi Salerno, ItalyInternal Medicine, Department of Medicine, Surgery and Dentistry “Scuola Medica Salernitana”, Pediatrics Section, University of Salerno, Baronissi Salerno, Italy; Corresponding author. Address: Via Salvador Allende 84081, Baronissi, Salerno, Italy; Tel.: +39 089 965028 - +39 3296239547.Internal Medicine, Department of Medicine, Surgery and Dentistry “Scuola Medica Salernitana”, Pediatrics Section, University of Salerno, Baronissi Salerno, ItalyInternal Medicine, Department of Medicine, Surgery and Dentistry “Scuola Medica Salernitana”, Pediatrics Section, University of Salerno, Baronissi Salerno, ItalyInternal Medicine, Department of Medicine, Surgery and Dentistry “Scuola Medica Salernitana”, Pediatrics Section, University of Salerno, Baronissi Salerno, Italyhttp://www.sciencedirect.com/science/article/pii/S2589555925001648 |
| spellingShingle | Claudia Mandato Mario Masarone Mariano Festa Pietro Torre Marcello Persico Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis JHEP Reports |
| title | Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis |
| title_full | Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis |
| title_fullStr | Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis |
| title_full_unstemmed | Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis |
| title_short | Odevixibat treatment reverses severe phenotype of PFIC in a young adult: A real-life experience beyond the genetic diagnosis |
| title_sort | odevixibat treatment reverses severe phenotype of pfic in a young adult a real life experience beyond the genetic diagnosis |
| url | http://www.sciencedirect.com/science/article/pii/S2589555925001648 |
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