Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case

Glycogen storage disease type IIIa (GSD IIIa) is a rare etiology among patients with adult-onset myopathy, which is typically associated with axonopathy rather than demyelination. We report a genetically and pathologically confirmed case that exhibited prominent electrophysiological hallmarks of dem...

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Main Authors: Zhou Xiajun, Zhong Xingxing, Gao Mingshi, Yue Dongyue, Qiao Kai, Wang Min, Zhi Nan, Cao Wenwei, Han Lu, Lu Jiahong, Zhu Wenhua, Zhao Chongbo, Guan Yangtai
Format: Article
Language:English
Published: De Gruyter 2025-04-01
Series:Open Medicine
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Online Access:https://doi.org/10.1515/med-2025-1172
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author Zhou Xiajun
Zhong Xingxing
Gao Mingshi
Yue Dongyue
Qiao Kai
Wang Min
Zhi Nan
Cao Wenwei
Han Lu
Lu Jiahong
Zhu Wenhua
Zhao Chongbo
Guan Yangtai
author_facet Zhou Xiajun
Zhong Xingxing
Gao Mingshi
Yue Dongyue
Qiao Kai
Wang Min
Zhi Nan
Cao Wenwei
Han Lu
Lu Jiahong
Zhu Wenhua
Zhao Chongbo
Guan Yangtai
author_sort Zhou Xiajun
collection DOAJ
description Glycogen storage disease type IIIa (GSD IIIa) is a rare etiology among patients with adult-onset myopathy, which is typically associated with axonopathy rather than demyelination. We report a genetically and pathologically confirmed case that exhibited prominent electrophysiological hallmarks of demyelination, including prolonged distal motor latency, temporal dispersion, prolonged F-waves, and conduction block. The presence of these diverse demyelinating characteristics in this context, excluding other factors, is infrequently reported, suggesting that glycogen accumulation may influence not only muscles but also potentially the myelin, thereby broadening our comprehension of this rare disease spectrum.
format Article
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institution Kabale University
issn 2391-5463
language English
publishDate 2025-04-01
publisher De Gruyter
record_format Article
series Open Medicine
spelling doaj-art-47bb393114764ceab3bc1a9f9c3cbf672025-08-20T03:52:16ZengDe GruyterOpen Medicine2391-54632025-04-012014466310.1515/med-2025-1172Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa caseZhou Xiajun0Zhong Xingxing1Gao Mingshi2Yue Dongyue3Qiao Kai4Wang Min5Zhi Nan6Cao Wenwei7Han Lu8Lu Jiahong9Zhu Wenhua10Zhao Chongbo11Guan Yangtai12Department of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaDepartment of Neurology, Northern Jiangsu People’s Hospital Affiliated to Yangzhou University, Jiangsu, 225000, ChinaDepartment of Pathology, Huashan Hospital, Fudan University, Shanghai, 200040, ChinaDepartment of Neurology, Jing’an District Center Hospital, Shanghai, 200040, ChinaDepartment of Neurology, and Huashan Rare Disease Center, Huashan Hospital, Fudan University, National Center for Neurological Disorders (NCND), Shanghai, 200040, ChinaDepartment of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaDepartment of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaDepartment of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaDepartment of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaDepartment of Neurology, and Huashan Rare Disease Center, Huashan Hospital, Fudan University, National Center for Neurological Disorders (NCND), Shanghai, 200040, ChinaDepartment of Neurology, and Huashan Rare Disease Center, Huashan Hospital, Fudan University, National Center for Neurological Disorders (NCND), Shanghai, 200040, ChinaDepartment of Neurology, and Huashan Rare Disease Center, Huashan Hospital, Fudan University, National Center for Neurological Disorders (NCND), Shanghai, 200040, ChinaDepartment of Neurology, Renji Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, 200127, ChinaGlycogen storage disease type IIIa (GSD IIIa) is a rare etiology among patients with adult-onset myopathy, which is typically associated with axonopathy rather than demyelination. We report a genetically and pathologically confirmed case that exhibited prominent electrophysiological hallmarks of demyelination, including prolonged distal motor latency, temporal dispersion, prolonged F-waves, and conduction block. The presence of these diverse demyelinating characteristics in this context, excluding other factors, is infrequently reported, suggesting that glycogen accumulation may influence not only muscles but also potentially the myelin, thereby broadening our comprehension of this rare disease spectrum.https://doi.org/10.1515/med-2025-1172glycogen storage disease type iiiglycogen debranching enzyme systemdemyelinating diseaseselectrophysiology
spellingShingle Zhou Xiajun
Zhong Xingxing
Gao Mingshi
Yue Dongyue
Qiao Kai
Wang Min
Zhi Nan
Cao Wenwei
Han Lu
Lu Jiahong
Zhu Wenhua
Zhao Chongbo
Guan Yangtai
Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
Open Medicine
glycogen storage disease type iii
glycogen debranching enzyme system
demyelinating diseases
electrophysiology
title Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
title_full Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
title_fullStr Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
title_full_unstemmed Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
title_short Diverse electrophysiological demyelinating features in a late-onset glycogen storage disease type IIIa case
title_sort diverse electrophysiological demyelinating features in a late onset glycogen storage disease type iiia case
topic glycogen storage disease type iii
glycogen debranching enzyme system
demyelinating diseases
electrophysiology
url https://doi.org/10.1515/med-2025-1172
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