Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data

Abstract Background Global healthcare disparities, stemming from organizational differences in healthcare systems, lead to variable availability and funding, resulting in a gap between recommended and implemented practices for interleukin (IL)-1-mediated autoinflammatory diseases. We aimed to assess...

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Main Authors: Marija Jelusic, Mario Sestan, Natasa Toplak, Constantin Tamas, Jelena Vojinovic, Zbigniew Zuber, Beata Wolska-Kusnierz, Mihaela Sparchez, Milos Jesenak, Skirmante Rusoniene, Valda Stanevica, Pavla Dolezalova, Liora Harel, Yosef Uziel, Marco Gattorno
Format: Article
Language:English
Published: BMC 2025-05-01
Series:Pediatric Rheumatology Online Journal
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Online Access:https://doi.org/10.1186/s12969-025-01105-3
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author Marija Jelusic
Mario Sestan
Natasa Toplak
Constantin Tamas
Jelena Vojinovic
Zbigniew Zuber
Beata Wolska-Kusnierz
Mihaela Sparchez
Milos Jesenak
Skirmante Rusoniene
Valda Stanevica
Pavla Dolezalova
Liora Harel
Yosef Uziel
Marco Gattorno
author_facet Marija Jelusic
Mario Sestan
Natasa Toplak
Constantin Tamas
Jelena Vojinovic
Zbigniew Zuber
Beata Wolska-Kusnierz
Mihaela Sparchez
Milos Jesenak
Skirmante Rusoniene
Valda Stanevica
Pavla Dolezalova
Liora Harel
Yosef Uziel
Marco Gattorno
author_sort Marija Jelusic
collection DOAJ
description Abstract Background Global healthcare disparities, stemming from organizational differences in healthcare systems, lead to variable availability and funding, resulting in a gap between recommended and implemented practices for interleukin (IL)-1-mediated autoinflammatory diseases. We aimed to assess diagnostic, treatment and follow-up options for these diseases in Central and Eastern European countries, comparing them with the 2021 recommendations of the European Alliance of Associations for Rheumatology (EULAR)/American College of Rheumatology (ACR). Methods In 2023, a structured collaborative effort was organized with representatives from 10 Central and Eastern European countries to address autoinflammatory diseases. The discussion focused on potential strategies to achieve the goals mentioned above. Results Almost all the participating countries have specialized centers for the diagnosis and treatment of autoinflammatory diseases and the care is provided either by rheumatologists and/or clinical immunologists. Genetic testing is available in all countries, but there is variation in the types of tests offered. Massive parallel sequencing panels for autoinflammatory diseases are available in all countries, with waiting periods for results ranging from 3 to 6 months in most cases. The availability of disease-specific laboratory assessments, such as S100 proteins, is limited. IL-1 inhibitors are available in all countries, but there are differences in practices regarding the licensing and reimbursement of anakinra and canakinumab based on specific indications or diagnoses. The age at which the transition process begins varies, but in most countries, it typically starts around the age of 18 or beyond and in majority of the participating countries there is no structured transition program. Conclusions Adherence to the 2021 EULAR/ACR recommendations for IL-1-mediated autoinflammatory diseases is achievable in Central and Eastern European countries. Determining the prevalence and incidence of these diseases in this region remains a persistent challenge for future research efforts, with the overarching goal of identifying new patients with autoinflammatory diseases.
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spelling doaj-art-46bb9c35ac8643a19abd1c76bcff42472025-08-20T02:29:26ZengBMCPediatric Rheumatology Online Journal1546-00962025-05-012311810.1186/s12969-025-01105-3Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world dataMarija Jelusic0Mario Sestan1Natasa Toplak2Constantin Tamas3Jelena Vojinovic4Zbigniew Zuber5Beata Wolska-Kusnierz6Mihaela Sparchez7Milos Jesenak8Skirmante Rusoniene9Valda Stanevica10Pavla Dolezalova11Liora Harel12Yosef Uziel13Marco Gattorno14Department of Paediatrics, University of Zagreb School of Medicine, Division of Clinical Immunology, Rheumatology and Allergology, Centre of Reference for Paediatric and Adolescent Rheumatology of Ministry of Health of the Republic Croatia, University Hospital Centre ZagrebDepartment of Paediatrics, University of Zagreb School of Medicine, Division of Clinical Immunology, Rheumatology and Allergology, Centre of Reference for Paediatric and Adolescent Rheumatology of Ministry of Health of the Republic Croatia, University Hospital Centre ZagrebDepartment of Allergology, Rheumatology and Clinical Immunology, University Children’s Hospital, University Medical Center Ljubljana, Ljubljana, Faculty of MedicineDivision of Pediatric Rheumatology and Immunology, Tuzolto Street Department, Pediatric Center, Semmelweis UniversityUniversity of Nis, Faculty of Medicine, University Clinical Center, Clinic of PediatricsDepartment of Pediatrics and Rheumatology, Andrzej Frycz Modrzewski Krakow University, St. Louis Children HospitalDepartment of Immunology, Children’s Memorial Health InstituteSecond Department of Paediatrics, Iuliu Hatieganu University of Medicine and PharmacyNational Centre for Periodic Fever Syndromes, Department of Pediatrics, Department of Pulmonology and Phthisiology, Department of Allergology and Clinical Immunology, Jessenius Faculty of Medicine, Comenius University in Bratislava, University Teaching Hospital in MartinClinic of Children’s Diseases, Institute of Clinical Medicine, Faculty of Medicine, Vilnius UniversityDepartment of Pediatrics, Riga Stradins UniversityCentre for Paediatric Rheumatology and Autoinflammatory Diseases ERN RITA, 1St Faculty of Medicine, Charles University and General University Hospital in PragueSackler Faculty of Medicine, Tel Aviv UniversityDepartment of Pediatrics, School of Medicine, Pediatric Rheumatology Unit, Meir Medical Center, Kfar Saba, and Tel Aviv UniversityUnit of Rheumatology and Autoinflammatory Diseases, IRCCS Istituto G. GasliniAbstract Background Global healthcare disparities, stemming from organizational differences in healthcare systems, lead to variable availability and funding, resulting in a gap between recommended and implemented practices for interleukin (IL)-1-mediated autoinflammatory diseases. We aimed to assess diagnostic, treatment and follow-up options for these diseases in Central and Eastern European countries, comparing them with the 2021 recommendations of the European Alliance of Associations for Rheumatology (EULAR)/American College of Rheumatology (ACR). Methods In 2023, a structured collaborative effort was organized with representatives from 10 Central and Eastern European countries to address autoinflammatory diseases. The discussion focused on potential strategies to achieve the goals mentioned above. Results Almost all the participating countries have specialized centers for the diagnosis and treatment of autoinflammatory diseases and the care is provided either by rheumatologists and/or clinical immunologists. Genetic testing is available in all countries, but there is variation in the types of tests offered. Massive parallel sequencing panels for autoinflammatory diseases are available in all countries, with waiting periods for results ranging from 3 to 6 months in most cases. The availability of disease-specific laboratory assessments, such as S100 proteins, is limited. IL-1 inhibitors are available in all countries, but there are differences in practices regarding the licensing and reimbursement of anakinra and canakinumab based on specific indications or diagnoses. The age at which the transition process begins varies, but in most countries, it typically starts around the age of 18 or beyond and in majority of the participating countries there is no structured transition program. Conclusions Adherence to the 2021 EULAR/ACR recommendations for IL-1-mediated autoinflammatory diseases is achievable in Central and Eastern European countries. Determining the prevalence and incidence of these diseases in this region remains a persistent challenge for future research efforts, with the overarching goal of identifying new patients with autoinflammatory diseases.https://doi.org/10.1186/s12969-025-01105-3Autoinflammatory diseasesInterleukin-1 mediated diseasesDiagnosisTreatmentMonitoringPatient-reported outcomes
spellingShingle Marija Jelusic
Mario Sestan
Natasa Toplak
Constantin Tamas
Jelena Vojinovic
Zbigniew Zuber
Beata Wolska-Kusnierz
Mihaela Sparchez
Milos Jesenak
Skirmante Rusoniene
Valda Stanevica
Pavla Dolezalova
Liora Harel
Yosef Uziel
Marco Gattorno
Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
Pediatric Rheumatology Online Journal
Autoinflammatory diseases
Interleukin-1 mediated diseases
Diagnosis
Treatment
Monitoring
Patient-reported outcomes
title Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
title_full Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
title_fullStr Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
title_full_unstemmed Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
title_short Diagnosis, management, and monitoring of interleukin-1 mediated diseases in Central and Eastern Europe: real-world data
title_sort diagnosis management and monitoring of interleukin 1 mediated diseases in central and eastern europe real world data
topic Autoinflammatory diseases
Interleukin-1 mediated diseases
Diagnosis
Treatment
Monitoring
Patient-reported outcomes
url https://doi.org/10.1186/s12969-025-01105-3
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