Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection

Abstract Severe pulmonary infection is a major threat to human health accompanied by substantial medical costs, prolonged inpatient requirements, and high mortality rates. New antimicrobial therapeutic strategies are urgently required to address the emergence of antibiotic resistance and persistent...

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Main Authors: Yue‐qing Zhou, Yun Shi, Ling Yang, Yu‐fen Sun, Yu‐fei Han, Zi‐xian Zhao, Yu‐jia Wang, Ying Liu, Yu Ma, Ting Zhang, Tao Ren, Tina P Dale, Nicholas R Forsyth, Fa‐guang Jin, Jie‐ming Qu, Wei Zuo, Jin‐fu Xu
Format: Article
Language:English
Published: Springer Nature 2019-11-01
Series:EMBO Molecular Medicine
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Online Access:https://doi.org/10.15252/emmm.201810233
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author Yue‐qing Zhou
Yun Shi
Ling Yang
Yu‐fen Sun
Yu‐fei Han
Zi‐xian Zhao
Yu‐jia Wang
Ying Liu
Yu Ma
Ting Zhang
Tao Ren
Tina P Dale
Nicholas R Forsyth
Fa‐guang Jin
Jie‐ming Qu
Wei Zuo
Jin‐fu Xu
author_facet Yue‐qing Zhou
Yun Shi
Ling Yang
Yu‐fen Sun
Yu‐fei Han
Zi‐xian Zhao
Yu‐jia Wang
Ying Liu
Yu Ma
Ting Zhang
Tao Ren
Tina P Dale
Nicholas R Forsyth
Fa‐guang Jin
Jie‐ming Qu
Wei Zuo
Jin‐fu Xu
author_sort Yue‐qing Zhou
collection DOAJ
description Abstract Severe pulmonary infection is a major threat to human health accompanied by substantial medical costs, prolonged inpatient requirements, and high mortality rates. New antimicrobial therapeutic strategies are urgently required to address the emergence of antibiotic resistance and persistent bacterial infections. In this study, we show that the constitutive expression of a native antimicrobial peptide LL‐37 in transgenic mice aids in clearing Pseudomonas aeruginosa (PAO1), a major pathogen of clinical pulmonary infection. Orthotopic transplantation of adult mouse distal airway stem cells (DASCs), genetically engineered to express LL‐37, into injured mouse lung foci enabled large‐scale incorporation of cells and long‐term release of the host defense peptide, protecting the mice from bacterial pneumonia and hypoxemia. Further, correlates of DASCs in adult humans were isolated, expanded, and genetically engineered to demonstrate successful construction of an anti‐infective artificial lung. Together, our stem cell‐based gene delivery therapeutic platform proposes a new strategy for addressing recurrent pulmonary infections with future translational opportunities.
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institution Kabale University
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language English
publishDate 2019-11-01
publisher Springer Nature
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series EMBO Molecular Medicine
spelling doaj-art-3ebe6e243af54e25b9c58a499c7dea522025-08-20T04:03:01ZengSpringer NatureEMBO Molecular Medicine1757-46761757-46842019-11-0112111610.15252/emmm.201810233Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infectionYue‐qing Zhou0Yun Shi1Ling Yang2Yu‐fen Sun3Yu‐fei Han4Zi‐xian Zhao5Yu‐jia Wang6Ying Liu7Yu Ma8Ting Zhang9Tao Ren10Tina P Dale11Nicholas R Forsyth12Fa‐guang Jin13Jie‐ming Qu14Wei Zuo15Jin‐fu Xu16Department of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineShanghai East Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineShanghai East Hospital, Tongji University School of MedicineShanghai East Hospital, Tongji University School of MedicineRegend Therapeutics Co. LtdShanghai East Hospital, Tongji University School of MedicineGuy Hilton Research Center, School of Pharmacy and Bioengineering, Keele UniversityGuy Hilton Research Center, School of Pharmacy and Bioengineering, Keele UniversityDepartment of Respiratory and Critical Care Medicine, Tangdu Hospital, Fourth Military Medical University of PLARuijin Hospital, Shanghai Jiaotong University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineDepartment of Respiratory and Critical Care Medicine, Clinical Translation Research Center, Shanghai Pulmonary Hospital, Tongji University School of MedicineAbstract Severe pulmonary infection is a major threat to human health accompanied by substantial medical costs, prolonged inpatient requirements, and high mortality rates. New antimicrobial therapeutic strategies are urgently required to address the emergence of antibiotic resistance and persistent bacterial infections. In this study, we show that the constitutive expression of a native antimicrobial peptide LL‐37 in transgenic mice aids in clearing Pseudomonas aeruginosa (PAO1), a major pathogen of clinical pulmonary infection. Orthotopic transplantation of adult mouse distal airway stem cells (DASCs), genetically engineered to express LL‐37, into injured mouse lung foci enabled large‐scale incorporation of cells and long‐term release of the host defense peptide, protecting the mice from bacterial pneumonia and hypoxemia. Further, correlates of DASCs in adult humans were isolated, expanded, and genetically engineered to demonstrate successful construction of an anti‐infective artificial lung. Together, our stem cell‐based gene delivery therapeutic platform proposes a new strategy for addressing recurrent pulmonary infections with future translational opportunities.https://doi.org/10.15252/emmm.201810233antimicrobial peptidedistal airway stem cellspulmonary infectiontransplantation
spellingShingle Yue‐qing Zhou
Yun Shi
Ling Yang
Yu‐fen Sun
Yu‐fei Han
Zi‐xian Zhao
Yu‐jia Wang
Ying Liu
Yu Ma
Ting Zhang
Tao Ren
Tina P Dale
Nicholas R Forsyth
Fa‐guang Jin
Jie‐ming Qu
Wei Zuo
Jin‐fu Xu
Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
EMBO Molecular Medicine
antimicrobial peptide
distal airway stem cells
pulmonary infection
transplantation
title Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
title_full Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
title_fullStr Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
title_full_unstemmed Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
title_short Genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
title_sort genetically engineered distal airway stem cell transplantation protects mice from pulmonary infection
topic antimicrobial peptide
distal airway stem cells
pulmonary infection
transplantation
url https://doi.org/10.15252/emmm.201810233
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