Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.

With more than 7,000 new HIV infections daily worldwide, there is an urgent need for non-vaccine biomedical prevention (nBP) strategies that are safe, effective, and acceptable. Clinical trials have demonstrated that pre-exposure prophylaxis (PrEP) with antiretrovirals (ARVs) can be effective at pre...

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Main Authors: Philippe A Gallay, Udayan Chatterji, Aaron Kirchhoff, Angel Gandarilla, Manjula Gunawardana, Richard B Pyles, Mark A Marzinke, John A Moss, Marc M Baum
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2017-01-01
Series:PLoS ONE
Online Access:https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0184303&type=printable
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author Philippe A Gallay
Udayan Chatterji
Aaron Kirchhoff
Angel Gandarilla
Manjula Gunawardana
Richard B Pyles
Mark A Marzinke
John A Moss
Marc M Baum
author_facet Philippe A Gallay
Udayan Chatterji
Aaron Kirchhoff
Angel Gandarilla
Manjula Gunawardana
Richard B Pyles
Mark A Marzinke
John A Moss
Marc M Baum
author_sort Philippe A Gallay
collection DOAJ
description With more than 7,000 new HIV infections daily worldwide, there is an urgent need for non-vaccine biomedical prevention (nBP) strategies that are safe, effective, and acceptable. Clinical trials have demonstrated that pre-exposure prophylaxis (PrEP) with antiretrovirals (ARVs) can be effective at preventing HIV infection. In contrast, other trials using the same ARVs failed to show consistent efficacy. Topical (vaginal and rectal) dosing is a promising regimen for HIV PrEP as it leads to low systematic drug exposure. A series of titration studies were carried out in bone marrow/liver/thymus (BLT) mice aimed at determining the adequate drug concentrations applied vaginally or rectally that offer protection against rectal or vaginal HIV challenge. The dose-response relationship of these agents was measured and showed that topical tenofovir disoproxil fumarate (TDF) and emtricitabine (FTC) can offer 100% protection against rectal or vaginal HIV challenges. From the challenge data, EC50 values of 4.6 μM for TDF and 0.6 μM for FTC for HIV vaginal administration and 6.1 μM TDF and 0.18 μM for FTC for rectal administration were obtained. These findings suggest that the BLT mouse model is highly suitable for studying the dose-response relationship in single and combination ARV studies of vaginal or rectal HIV exposure. Application of this sensitive HIV infection model to more complex binary and ternary ARV combinations, particularly where agents have different mechanisms of action, should allow selection of optimal ARV combinations to be advanced into pre-clinical and clinical development as nBP products.
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spelling doaj-art-3d41b996c19f468aa0856e3cda9695312025-08-20T02:03:47ZengPublic Library of Science (PLoS)PLoS ONE1932-62032017-01-01129e018430310.1371/journal.pone.0184303Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.Philippe A GallayUdayan ChatterjiAaron KirchhoffAngel GandarillaManjula GunawardanaRichard B PylesMark A MarzinkeJohn A MossMarc M BaumWith more than 7,000 new HIV infections daily worldwide, there is an urgent need for non-vaccine biomedical prevention (nBP) strategies that are safe, effective, and acceptable. Clinical trials have demonstrated that pre-exposure prophylaxis (PrEP) with antiretrovirals (ARVs) can be effective at preventing HIV infection. In contrast, other trials using the same ARVs failed to show consistent efficacy. Topical (vaginal and rectal) dosing is a promising regimen for HIV PrEP as it leads to low systematic drug exposure. A series of titration studies were carried out in bone marrow/liver/thymus (BLT) mice aimed at determining the adequate drug concentrations applied vaginally or rectally that offer protection against rectal or vaginal HIV challenge. The dose-response relationship of these agents was measured and showed that topical tenofovir disoproxil fumarate (TDF) and emtricitabine (FTC) can offer 100% protection against rectal or vaginal HIV challenges. From the challenge data, EC50 values of 4.6 μM for TDF and 0.6 μM for FTC for HIV vaginal administration and 6.1 μM TDF and 0.18 μM for FTC for rectal administration were obtained. These findings suggest that the BLT mouse model is highly suitable for studying the dose-response relationship in single and combination ARV studies of vaginal or rectal HIV exposure. Application of this sensitive HIV infection model to more complex binary and ternary ARV combinations, particularly where agents have different mechanisms of action, should allow selection of optimal ARV combinations to be advanced into pre-clinical and clinical development as nBP products.https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0184303&type=printable
spellingShingle Philippe A Gallay
Udayan Chatterji
Aaron Kirchhoff
Angel Gandarilla
Manjula Gunawardana
Richard B Pyles
Mark A Marzinke
John A Moss
Marc M Baum
Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
PLoS ONE
title Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
title_full Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
title_fullStr Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
title_full_unstemmed Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
title_short Prevention of vaginal and rectal HIV transmission by antiretroviral combinations in humanized mice.
title_sort prevention of vaginal and rectal hiv transmission by antiretroviral combinations in humanized mice
url https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0184303&type=printable
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