Hematopoietic stem cell transplantation in pediatric patients with type VI mucopolysaccharidosis

Background It is uncertain whether hematopoietic stem cell transplantation (HSCT), versus standard enzyme replacement therapy (ERT), is effective for type VI mucopolysaccharidosis (MPS VI). Purpose New related advances in HSCT prompted an examination of the transplant procedures performed in a recen...

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Bibliographic Details
Main Authors: Vedat Uygun, Koray Yalçın, Hayriye Daloğlu, Seda Öztürkmen, Suna Çelen, Suleimen Zhumatayev, Gülsün Karasu, Akif Yeşilipek
Format: Article
Language:English
Published: The Korean Pediatric Society 2025-08-01
Series:Clinical and Experimental Pediatrics
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Online Access:http://www.e-cep.org/upload/pdf/cep-2024-02033.pdf
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