Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma

Abstract We present a case of extensive and bulky pediatric metastatic melanoma originating in the head and neck which markedly responded to combination therapy with anti-programmed cell death (PD-1) inhibition and consolidative personalized ultra-fractionated stereotactic adaptive radiotherapy (PUL...

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Main Authors: Kyra L. McCarty, Tanya Watt, Tu D. Dan, Robert D. Timmerman, Kiran A. Kumar
Format: Article
Language:English
Published: BMC 2025-08-01
Series:Radiation Oncology
Subjects:
Online Access:https://doi.org/10.1186/s13014-025-02691-y
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author Kyra L. McCarty
Tanya Watt
Tu D. Dan
Robert D. Timmerman
Kiran A. Kumar
author_facet Kyra L. McCarty
Tanya Watt
Tu D. Dan
Robert D. Timmerman
Kiran A. Kumar
author_sort Kyra L. McCarty
collection DOAJ
description Abstract We present a case of extensive and bulky pediatric metastatic melanoma originating in the head and neck which markedly responded to combination therapy with anti-programmed cell death (PD-1) inhibition and consolidative personalized ultra-fractionated stereotactic adaptive radiotherapy (PULSAR). After surgical debulking with neck dissection, the patient was initially treated with anti-PD-1 and anti-cytotoxic T-lymphocyte associated protein 4 (CTLA-4) dual checkpoint blockade immunotherapy, but quickly had disease progression. He was transitioned to a different anti-PD-1 immunotherapy in combination with tyrosine kinase inhibitors in conjunction with consolidative local therapy using PULSAR. This combination therapy achieved tumor response and progression-free status for one year before further disease progression at a separate site in the mediastinum. Due to otherwise good disease control, single agent anti-PD-1 immunotherapy was continued and salvage PULSAR was administered to the progressive site, again resulting in tumor response and progression-free status for 6 months. None of the bulkier sites of gross disease had local progression after combination therapy. This case suggests that the synergistic effect of PULSAR and anti-PD-1 immunotherapy is efficacious for relapsed or refractory metastatic melanoma in pediatric patients. Clinical trial number: not applicable.
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spelling doaj-art-392e51dd46c94d2e96be2e528d5636622025-08-24T11:42:09ZengBMCRadiation Oncology1748-717X2025-08-012011710.1186/s13014-025-02691-yUse of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanomaKyra L. McCarty0Tanya Watt1Tu D. Dan2Robert D. Timmerman3Kiran A. Kumar4Division of Pediatric Hematology and Oncology, UT Southwestern Medical CenterDivision of Pediatric Hematology and Oncology, UT Southwestern Medical CenterDepartment of Radiation Oncology, UT Southwestern Medical CenterDepartment of Radiation Oncology, UT Southwestern Medical CenterDepartment of Radiation Oncology, UT Southwestern Medical CenterAbstract We present a case of extensive and bulky pediatric metastatic melanoma originating in the head and neck which markedly responded to combination therapy with anti-programmed cell death (PD-1) inhibition and consolidative personalized ultra-fractionated stereotactic adaptive radiotherapy (PULSAR). After surgical debulking with neck dissection, the patient was initially treated with anti-PD-1 and anti-cytotoxic T-lymphocyte associated protein 4 (CTLA-4) dual checkpoint blockade immunotherapy, but quickly had disease progression. He was transitioned to a different anti-PD-1 immunotherapy in combination with tyrosine kinase inhibitors in conjunction with consolidative local therapy using PULSAR. This combination therapy achieved tumor response and progression-free status for one year before further disease progression at a separate site in the mediastinum. Due to otherwise good disease control, single agent anti-PD-1 immunotherapy was continued and salvage PULSAR was administered to the progressive site, again resulting in tumor response and progression-free status for 6 months. None of the bulkier sites of gross disease had local progression after combination therapy. This case suggests that the synergistic effect of PULSAR and anti-PD-1 immunotherapy is efficacious for relapsed or refractory metastatic melanoma in pediatric patients. Clinical trial number: not applicable.https://doi.org/10.1186/s13014-025-02691-yMetastatic melanomaPULSARPembrolizumabanti-PD-1anti-CTLA-4BRAF Inhibition
spellingShingle Kyra L. McCarty
Tanya Watt
Tu D. Dan
Robert D. Timmerman
Kiran A. Kumar
Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
Radiation Oncology
Metastatic melanoma
PULSAR
Pembrolizumab
anti-PD-1
anti-CTLA-4
BRAF Inhibition
title Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
title_full Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
title_fullStr Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
title_full_unstemmed Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
title_short Use of PULSAR (personalized ultra-fractionated stereotactic adaptive radiotherapy) as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
title_sort use of pulsar personalized ultra fractionated stereotactic adaptive radiotherapy as consolidation with immune checkpoint inhibition in the treatment of pediatric metastatic melanoma
topic Metastatic melanoma
PULSAR
Pembrolizumab
anti-PD-1
anti-CTLA-4
BRAF Inhibition
url https://doi.org/10.1186/s13014-025-02691-y
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