Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.

Homologous recombination (HR) faithfully restores DNA double-strand breaks. Defects in this HR repair pathway are associated with cancer predisposition. In genetic engineering, HR has been used extensively to study gene function and it represents an ideal method of gene therapy for single gene disor...

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Main Authors: Alejandra Bernardi, Dino Gobelli, Julia Serna, Paulina Nawrocka, Gabriel March-Rosselló, Antonio Orduña, Piotr Kozlowski, María Simarro, Miguel A de la Fuente
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2021-01-01
Series:PLoS ONE
Online Access:https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0237413&type=printable
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author Alejandra Bernardi
Dino Gobelli
Julia Serna
Paulina Nawrocka
Gabriel March-Rosselló
Antonio Orduña
Piotr Kozlowski
María Simarro
Miguel A de la Fuente
author_facet Alejandra Bernardi
Dino Gobelli
Julia Serna
Paulina Nawrocka
Gabriel March-Rosselló
Antonio Orduña
Piotr Kozlowski
María Simarro
Miguel A de la Fuente
author_sort Alejandra Bernardi
collection DOAJ
description Homologous recombination (HR) faithfully restores DNA double-strand breaks. Defects in this HR repair pathway are associated with cancer predisposition. In genetic engineering, HR has been used extensively to study gene function and it represents an ideal method of gene therapy for single gene disorders. Here, we present a novel assay to measure HR in living cells. The HR substrate consisted of a non-fluorescent 3' truncated form of the eGFP gene and was integrated into the AAVS1 locus, known as a safe harbor. The donor DNA template comprised a 5' truncated eGFP copy and was delivered via AAV particles. HR mediated repair restored full-length eGFP coding sequence, resulting in eGFP+ cells. The utility of our assay in quantifying HR events was validated by exploring the impact of the overexpression of HR promoters and the siRNA-mediated silencing of genes known to play a role in DNA repair on the frequency of HR. We conclude that this novel assay represents a useful tool to further investigate the mechanisms that control HR and test continually emerging tools for HR-mediated genome editing.
format Article
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institution OA Journals
issn 1932-6203
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publishDate 2021-01-01
publisher Public Library of Science (PLoS)
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series PLoS ONE
spelling doaj-art-388a77dad91c4ac9aab9c5687726972a2025-08-20T02:17:48ZengPublic Library of Science (PLoS)PLoS ONE1932-62032021-01-01164e023741310.1371/journal.pone.0237413Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.Alejandra BernardiDino GobelliJulia SernaPaulina NawrockaGabriel March-RossellóAntonio OrduñaPiotr KozlowskiMaría SimarroMiguel A de la FuenteHomologous recombination (HR) faithfully restores DNA double-strand breaks. Defects in this HR repair pathway are associated with cancer predisposition. In genetic engineering, HR has been used extensively to study gene function and it represents an ideal method of gene therapy for single gene disorders. Here, we present a novel assay to measure HR in living cells. The HR substrate consisted of a non-fluorescent 3' truncated form of the eGFP gene and was integrated into the AAVS1 locus, known as a safe harbor. The donor DNA template comprised a 5' truncated eGFP copy and was delivered via AAV particles. HR mediated repair restored full-length eGFP coding sequence, resulting in eGFP+ cells. The utility of our assay in quantifying HR events was validated by exploring the impact of the overexpression of HR promoters and the siRNA-mediated silencing of genes known to play a role in DNA repair on the frequency of HR. We conclude that this novel assay represents a useful tool to further investigate the mechanisms that control HR and test continually emerging tools for HR-mediated genome editing.https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0237413&type=printable
spellingShingle Alejandra Bernardi
Dino Gobelli
Julia Serna
Paulina Nawrocka
Gabriel March-Rosselló
Antonio Orduña
Piotr Kozlowski
María Simarro
Miguel A de la Fuente
Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
PLoS ONE
title Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
title_full Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
title_fullStr Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
title_full_unstemmed Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
title_short Novel fluorescent-based reporter cell line engineered for monitoring homologous recombination events.
title_sort novel fluorescent based reporter cell line engineered for monitoring homologous recombination events
url https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0237413&type=printable
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