O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH

Conflict of interest: No Introduction and Objectives: In a recent article from the American Journal of Human Genetics, the genetic behavior of variants associated with Wilson's Disease (WD) is analyzed, alongside the worldwide discovery of the responsible gene. The variant c.3809A>G (p.Asn12...

Full description

Saved in:
Bibliographic Details
Main Authors: Danny Alvarado, Jorge Andres Herrera Corrales, Mildred Jimenez, Karina Hidalgo, Fernanda Vasquez, Francisco Vargas, Jorge Vargas, Francisco Hevia Urrutia
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Annals of Hepatology
Online Access:http://www.sciencedirect.com/science/article/pii/S1665268124003934
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850112163598827520
author Danny Alvarado
Jorge Andres Herrera Corrales
Mildred Jimenez
Karina Hidalgo
Fernanda Vasquez
Francisco Vargas
Jorge Vargas
Francisco Hevia Urrutia
author_facet Danny Alvarado
Jorge Andres Herrera Corrales
Mildred Jimenez
Karina Hidalgo
Fernanda Vasquez
Francisco Vargas
Jorge Vargas
Francisco Hevia Urrutia
author_sort Danny Alvarado
collection DOAJ
description Conflict of interest: No Introduction and Objectives: In a recent article from the American Journal of Human Genetics, the genetic behavior of variants associated with Wilson's Disease (WD) is analyzed, alongside the worldwide discovery of the responsible gene. The variant c.3809A>G (p.Asn1270Ser) is highlighted, with a prevalence of 61% in Costa Rica, differing from that observed in Europe and the United States, and originally described in Sicily. The Genetics Center of the National Children's Hospital has been instrumental in identifying a specific genetic pattern among Costa Ricans with WD. Additionally, a novel worldwide variant in heterozygosity has been discovered in Nicaraguan patients, solidifying Costa Rica as a country with a high incidence of WD and significant contributions to the genetic study of the disease, which has documented over 1161 pathogenic variants. Objective: To analyze and describe the genetic spectrum of these variants in Costa Rica over the past two years, aiming to establish a comprehensive genetic map in a population with a high incidence of WD. Patients / Materials and Methods: Molecular Sequencing (Sanger NGS) for molecular confirmation, as well as MLPA techniques and Copy Number Variations (CNVs) analysis. Results and Discussion: During the period (2022-2023), 86 patients with WD variants were identified, including 19 homozygotes, 11 compound heterozygotes, and 56 carriers. There was a significant gender distribution, with a female predominance among homozygotes (58%) and male predominance among compound heterozygotes (64%). The ages of the patients varied widely, with an average age of 20 years for homozygotes and 21 years for compound heterozygotes. Multiple genetic variants were identified in genes such as ATP7B, including p.N1270S and others. Conclusions: The importance of genetic research in understanding complex hereditary diseases like WD is underscored. The high prevalence of the c.3809A>G variant in Costa Rica highlights regional genetic diversity and the need to adapt diagnostic and treatment strategies to the specific genetic characteristics of each population.
format Article
id doaj-art-3614c364ecb244f2a0f1f0e3d4bef67f
institution OA Journals
issn 1665-2681
language English
publishDate 2024-12-01
publisher Elsevier
record_format Article
series Annals of Hepatology
spelling doaj-art-3614c364ecb244f2a0f1f0e3d4bef67f2025-08-20T02:37:28ZengElsevierAnnals of Hepatology1665-26812024-12-012910161010.1016/j.aohep.2024.101610O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACHDanny Alvarado0Jorge Andres Herrera Corrales1Mildred Jimenez2Karina Hidalgo3Fernanda Vasquez4Francisco Vargas5Jorge Vargas6Francisco Hevia Urrutia7CAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaCAJA COSTARRICENSE DEL SEGURO SOCIAL, San Jose, Costa RicaConflict of interest: No Introduction and Objectives: In a recent article from the American Journal of Human Genetics, the genetic behavior of variants associated with Wilson's Disease (WD) is analyzed, alongside the worldwide discovery of the responsible gene. The variant c.3809A>G (p.Asn1270Ser) is highlighted, with a prevalence of 61% in Costa Rica, differing from that observed in Europe and the United States, and originally described in Sicily. The Genetics Center of the National Children's Hospital has been instrumental in identifying a specific genetic pattern among Costa Ricans with WD. Additionally, a novel worldwide variant in heterozygosity has been discovered in Nicaraguan patients, solidifying Costa Rica as a country with a high incidence of WD and significant contributions to the genetic study of the disease, which has documented over 1161 pathogenic variants. Objective: To analyze and describe the genetic spectrum of these variants in Costa Rica over the past two years, aiming to establish a comprehensive genetic map in a population with a high incidence of WD. Patients / Materials and Methods: Molecular Sequencing (Sanger NGS) for molecular confirmation, as well as MLPA techniques and Copy Number Variations (CNVs) analysis. Results and Discussion: During the period (2022-2023), 86 patients with WD variants were identified, including 19 homozygotes, 11 compound heterozygotes, and 56 carriers. There was a significant gender distribution, with a female predominance among homozygotes (58%) and male predominance among compound heterozygotes (64%). The ages of the patients varied widely, with an average age of 20 years for homozygotes and 21 years for compound heterozygotes. Multiple genetic variants were identified in genes such as ATP7B, including p.N1270S and others. Conclusions: The importance of genetic research in understanding complex hereditary diseases like WD is underscored. The high prevalence of the c.3809A>G variant in Costa Rica highlights regional genetic diversity and the need to adapt diagnostic and treatment strategies to the specific genetic characteristics of each population.http://www.sciencedirect.com/science/article/pii/S1665268124003934
spellingShingle Danny Alvarado
Jorge Andres Herrera Corrales
Mildred Jimenez
Karina Hidalgo
Fernanda Vasquez
Francisco Vargas
Jorge Vargas
Francisco Hevia Urrutia
O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
Annals of Hepatology
title O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
title_full O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
title_fullStr O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
title_full_unstemmed O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
title_short O-12 DECIPHERING WILSON'S DISEASE IN COSTA RICA: AN INNOVATIVE GENETIC APPROACH
title_sort o 12 deciphering wilson s disease in costa rica an innovative genetic approach
url http://www.sciencedirect.com/science/article/pii/S1665268124003934
work_keys_str_mv AT dannyalvarado o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT jorgeandresherreracorrales o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT mildredjimenez o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT karinahidalgo o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT fernandavasquez o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT franciscovargas o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT jorgevargas o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach
AT franciscoheviaurrutia o12decipheringwilsonsdiseaseincostaricaaninnovativegeneticapproach