Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease

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Main Authors: Barry J. Byrne, Giancarlo Parenti, Benedikt Schoser, Ans T. van der Ploeg, Hung Do, Brian Fox, Mitchell Goldman, Franklin K. Johnson, Jia Kang, Nickita Mehta, John Mondick, M. Osman Sheikh, Sheela Sitaraman Das, Steven Tuske, Jon Brudvig, Jill M. Weimer, Tahseen Mozaffar
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-01-01
Series:Frontiers in Neurology
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Online Access:https://www.frontiersin.org/articles/10.3389/fneur.2024.1540452/full
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author Barry J. Byrne
Giancarlo Parenti
Giancarlo Parenti
Benedikt Schoser
Ans T. van der Ploeg
Hung Do
Brian Fox
Mitchell Goldman
Franklin K. Johnson
Jia Kang
Nickita Mehta
John Mondick
M. Osman Sheikh
Sheela Sitaraman Das
Steven Tuske
Jon Brudvig
Jill M. Weimer
Tahseen Mozaffar
author_facet Barry J. Byrne
Giancarlo Parenti
Giancarlo Parenti
Benedikt Schoser
Ans T. van der Ploeg
Hung Do
Brian Fox
Mitchell Goldman
Franklin K. Johnson
Jia Kang
Nickita Mehta
John Mondick
M. Osman Sheikh
Sheela Sitaraman Das
Steven Tuske
Jon Brudvig
Jill M. Weimer
Tahseen Mozaffar
author_sort Barry J. Byrne
collection DOAJ
format Article
id doaj-art-3600628dfa994bfab01c6f18d64330fe
institution Kabale University
issn 1664-2295
language English
publishDate 2025-01-01
publisher Frontiers Media S.A.
record_format Article
series Frontiers in Neurology
spelling doaj-art-3600628dfa994bfab01c6f18d64330fe2025-01-03T05:10:18ZengFrontiers Media S.A.Frontiers in Neurology1664-22952025-01-011510.3389/fneur.2024.15404521540452Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe diseaseBarry J. Byrne0Giancarlo Parenti1Giancarlo Parenti2Benedikt Schoser3Ans T. van der Ploeg4Hung Do5Brian Fox6Mitchell Goldman7Franklin K. Johnson8Jia Kang9Nickita Mehta10John Mondick11M. Osman Sheikh12Sheela Sitaraman Das13Steven Tuske14Jon Brudvig15Jill M. Weimer16Tahseen Mozaffar17Department of Pediatrics in the College of Medicine, University of Florida, Gainesville, FL, United StatesMetabolic Unit, Department of Translational Medical Sciences, University of Naples Federico II, Naples, ItalyTelethon Institute of Genetics and Medicine, Pozzuoli, ItalyFriedrich-Baur-Institute, Department of Neurology, LMU University Hospital, LMU Munich, Munich, GermanyErasmus MC University Medical Center, Rotterdam, NetherlandsM6P-Therapeutics, St Louis, MO, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesMetrum Research Group, Tariffville, CT, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesIncyte Corporation, Wilmington, DE, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United StatesAmicus Therapeutics, Inc., Princeton, NJ, United States0Department of Neurology, University of California, Irvine, Irvine, CA, United Stateshttps://www.frontiersin.org/articles/10.3389/fneur.2024.1540452/fullPompe diseaseglycogen storage disease type IIlysosomal storage disordersenzyme replacement therapyn-butyldeoxynojirimycin
spellingShingle Barry J. Byrne
Giancarlo Parenti
Giancarlo Parenti
Benedikt Schoser
Ans T. van der Ploeg
Hung Do
Brian Fox
Mitchell Goldman
Franklin K. Johnson
Jia Kang
Nickita Mehta
John Mondick
M. Osman Sheikh
Sheela Sitaraman Das
Steven Tuske
Jon Brudvig
Jill M. Weimer
Tahseen Mozaffar
Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
Frontiers in Neurology
Pompe disease
glycogen storage disease type II
lysosomal storage disorders
enzyme replacement therapy
n-butyldeoxynojirimycin
title Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
title_full Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
title_fullStr Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
title_full_unstemmed Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
title_short Corrigendum: Cipaglucosidase alfa plus miglustat: linking mechanism of action to clinical outcomes in late-onset Pompe disease
title_sort corrigendum cipaglucosidase alfa plus miglustat linking mechanism of action to clinical outcomes in late onset pompe disease
topic Pompe disease
glycogen storage disease type II
lysosomal storage disorders
enzyme replacement therapy
n-butyldeoxynojirimycin
url https://www.frontiersin.org/articles/10.3389/fneur.2024.1540452/full
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