Discovery of EP4 antagonists with image-guided explainable deep learning workflow

In target-based drug design, the manual creation of a poor initial compound library, the time-consuming wet-laboratory experimental screening method, and the weak explainability of their activity against compounds significantly limit the efficiency of discovering novel therapeutics. Here we propose...

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Main Authors: Ma Pengsen, Cheng Zhiyuan, Cheng Zhixiang, Wang Yijie, Chai Xiaolei, Feng Bo, Xiang Hongxin, Zeng Li, Liu Xueming, Li Pengyong, Wei Leyi, Zou Quan, Liu Mingyao, Zeng Xiangxiang, Lu Weiqiang
Format: Article
Language:English
Published: Science Press 2025-06-01
Series:National Science Open
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Online Access:https://www.sciengine.com/doi/10.1360/nso/20240015
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Summary:In target-based drug design, the manual creation of a poor initial compound library, the time-consuming wet-laboratory experimental screening method, and the weak explainability of their activity against compounds significantly limit the efficiency of discovering novel therapeutics. Here we propose an image-guided, interpretability deep learning workflow, named LeadDisFlow, to enable rapid, accurate target drug discovery. Using LeadDisFlow, we identified four potent antagonists with single-nanomolar antagonistic activity against PGE<sub>2</sub> receptor subtype 4 (EP4), a promising target for tumor immunotherapy. Remarkably, the most potent EP4 antagonist, ZY001, demonstrated an IC<sub>50</sub> value of (0.51 ± 0.02) nM, along with high selectivity. Furthermore, ZY001 effectively impaired the PGE<sub>2</sub>-induced gene expression of a panel of immunosuppressive molecules in macrophages. The workflow facilitates the discovery of potent EP4 antagonists that enhance anti-tumor immune response, and provides a convenient and quick approach to discover promising therapeutics for a specific drug target.
ISSN:2097-1168