High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.

SARS-CoV-2 has caused a global pandemic, and has taken over 1.7 million lives as of mid-December, 2020. Although great progress has been made in the development of effective countermeasures, with several pharmaceutical companies approved or poised to deliver vaccines to market, there is still an unm...

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Main Authors: Ryan Choi, Mowei Zhou, Roger Shek, Jesse W Wilson, Logan Tillery, Justin K Craig, Indraneel A Salukhe, Sarah E Hickson, Neeraj Kumar, Rhema M James, Garry W Buchko, Ruilian Wu, Sydney Huff, Tu-Trinh Nguyen, Brett L Hurst, Sara Cherry, Lynn K Barrett, Jennifer L Hyde, Wesley C Van Voorhis
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2021-01-01
Series:PLoS ONE
Online Access:https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0250019&type=printable
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author Ryan Choi
Mowei Zhou
Roger Shek
Jesse W Wilson
Logan Tillery
Justin K Craig
Indraneel A Salukhe
Sarah E Hickson
Neeraj Kumar
Rhema M James
Garry W Buchko
Ruilian Wu
Sydney Huff
Tu-Trinh Nguyen
Brett L Hurst
Sara Cherry
Lynn K Barrett
Jennifer L Hyde
Wesley C Van Voorhis
author_facet Ryan Choi
Mowei Zhou
Roger Shek
Jesse W Wilson
Logan Tillery
Justin K Craig
Indraneel A Salukhe
Sarah E Hickson
Neeraj Kumar
Rhema M James
Garry W Buchko
Ruilian Wu
Sydney Huff
Tu-Trinh Nguyen
Brett L Hurst
Sara Cherry
Lynn K Barrett
Jennifer L Hyde
Wesley C Van Voorhis
author_sort Ryan Choi
collection DOAJ
description SARS-CoV-2 has caused a global pandemic, and has taken over 1.7 million lives as of mid-December, 2020. Although great progress has been made in the development of effective countermeasures, with several pharmaceutical companies approved or poised to deliver vaccines to market, there is still an unmet need of essential antiviral drugs with therapeutic impact for the treatment of moderate-to-severe COVID-19. Towards this goal, a high-throughput assay was used to screen SARS-CoV-2 nsp15 uracil-dependent endonuclease (endoU) function against 13 thousand compounds from drug and lead repurposing compound libraries. While over 80% of initial hit compounds were pan-assay inhibitory compounds, three hits were confirmed as nsp15 endoU inhibitors in the 1-20 μM range in vitro. Furthermore, Exebryl-1, a ß-amyloid anti-aggregation molecule for Alzheimer's therapy, was shown to have antiviral activity between 10 to 66 μM, in Vero 76, Caco-2, and Calu-3 cells. Although the inhibitory concentrations determined for Exebryl-1 exceed those recommended for therapeutic intervention, our findings show great promise for further optimization of Exebryl-1 as an nsp15 endoU inhibitor and as a SARS-CoV-2 antiviral.
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institution Kabale University
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spelling doaj-art-2fda872016ce488d907c534ff63b8ecb2025-08-20T03:25:35ZengPublic Library of Science (PLoS)PLoS ONE1932-62032021-01-01164e025001910.1371/journal.pone.0250019High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.Ryan ChoiMowei ZhouRoger ShekJesse W WilsonLogan TilleryJustin K CraigIndraneel A SalukheSarah E HicksonNeeraj KumarRhema M JamesGarry W BuchkoRuilian WuSydney HuffTu-Trinh NguyenBrett L HurstSara CherryLynn K BarrettJennifer L HydeWesley C Van VoorhisSARS-CoV-2 has caused a global pandemic, and has taken over 1.7 million lives as of mid-December, 2020. Although great progress has been made in the development of effective countermeasures, with several pharmaceutical companies approved or poised to deliver vaccines to market, there is still an unmet need of essential antiviral drugs with therapeutic impact for the treatment of moderate-to-severe COVID-19. Towards this goal, a high-throughput assay was used to screen SARS-CoV-2 nsp15 uracil-dependent endonuclease (endoU) function against 13 thousand compounds from drug and lead repurposing compound libraries. While over 80% of initial hit compounds were pan-assay inhibitory compounds, three hits were confirmed as nsp15 endoU inhibitors in the 1-20 μM range in vitro. Furthermore, Exebryl-1, a ß-amyloid anti-aggregation molecule for Alzheimer's therapy, was shown to have antiviral activity between 10 to 66 μM, in Vero 76, Caco-2, and Calu-3 cells. Although the inhibitory concentrations determined for Exebryl-1 exceed those recommended for therapeutic intervention, our findings show great promise for further optimization of Exebryl-1 as an nsp15 endoU inhibitor and as a SARS-CoV-2 antiviral.https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0250019&type=printable
spellingShingle Ryan Choi
Mowei Zhou
Roger Shek
Jesse W Wilson
Logan Tillery
Justin K Craig
Indraneel A Salukhe
Sarah E Hickson
Neeraj Kumar
Rhema M James
Garry W Buchko
Ruilian Wu
Sydney Huff
Tu-Trinh Nguyen
Brett L Hurst
Sara Cherry
Lynn K Barrett
Jennifer L Hyde
Wesley C Van Voorhis
High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
PLoS ONE
title High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
title_full High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
title_fullStr High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
title_full_unstemmed High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
title_short High-throughput screening of the ReFRAME, Pandemic Box, and COVID Box drug repurposing libraries against SARS-CoV-2 nsp15 endoribonuclease to identify small-molecule inhibitors of viral activity.
title_sort high throughput screening of the reframe pandemic box and covid box drug repurposing libraries against sars cov 2 nsp15 endoribonuclease to identify small molecule inhibitors of viral activity
url https://journals.plos.org/plosone/article/file?id=10.1371/journal.pone.0250019&type=printable
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