The use of Sirolimus for an unresectable and refractory venous malformation: A case series

Vascular malformations (VM) may become symptomatic and extensive, leading to deranged coagulation and bleeding. Sirolimus®, an antiangiogenic agent, has recently emerged as treatment for VM. We report its short-term outcomes for VMs of the extremities. Case 1: A 47-year-old female reported left fore...

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Main Authors: Daniela Kristina Carolino, MD, Keiichi Muramatsu, MD, Yasuhiro Tani, MD, Hideaki Sugimoto, MD, Masaya Ueda, MD
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Radiology Case Reports
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Online Access:http://www.sciencedirect.com/science/article/pii/S1930043325002262
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author Daniela Kristina Carolino, MD
Keiichi Muramatsu, MD
Yasuhiro Tani, MD
Hideaki Sugimoto, MD
Masaya Ueda, MD
author_facet Daniela Kristina Carolino, MD
Keiichi Muramatsu, MD
Yasuhiro Tani, MD
Hideaki Sugimoto, MD
Masaya Ueda, MD
author_sort Daniela Kristina Carolino, MD
collection DOAJ
description Vascular malformations (VM) may become symptomatic and extensive, leading to deranged coagulation and bleeding. Sirolimus®, an antiangiogenic agent, has recently emerged as treatment for VM. We report its short-term outcomes for VMs of the extremities. Case 1: A 47-year-old female reported left forearm pain. MRI confirmed a VM. Lesion shrinkage and pain relief were not achieved despite sclerotherapy. After 5 months on Sirolimus®, improved pain, decreased forearm circumference and decreased lesion size on MRI were observed. Case 2: 62-year-old male reported left knee pain. MRI and biopsy confirmed a VM. After 3 months on Sirolimus®, improved pain, decreased leg circumference, and decreased lesion size on MRI were observed. Our series demonstrates that Sirolimus® is efficacious in downsizing VMs with resultant symptom relief in the short-term. Other series has likewise shown effectivity in extensive and refractory lesions, with benefits outweighing side effects.
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series Radiology Case Reports
spelling doaj-art-2d4c213207594629bcd894b5eadbfd192025-08-20T02:12:09ZengElsevierRadiology Case Reports1930-04332025-06-012063081308510.1016/j.radcr.2025.03.016The use of Sirolimus for an unresectable and refractory venous malformation: A case seriesDaniela Kristina Carolino, MD0Keiichi Muramatsu, MD1Yasuhiro Tani, MD2Hideaki Sugimoto, MD3Masaya Ueda, MD4Department of Orthopedic Surgery, Nagato General Hospital, 85 Higashi-Fukawa, Yamaguchi 759-4194, Nagato, JapanCorresponding author.; Department of Orthopedic Surgery, Nagato General Hospital, 85 Higashi-Fukawa, Yamaguchi 759-4194, Nagato, JapanDepartment of Orthopedic Surgery, Nagato General Hospital, 85 Higashi-Fukawa, Yamaguchi 759-4194, Nagato, JapanDepartment of Orthopedic Surgery, Nagato General Hospital, 85 Higashi-Fukawa, Yamaguchi 759-4194, Nagato, JapanDepartment of Orthopedic Surgery, Nagato General Hospital, 85 Higashi-Fukawa, Yamaguchi 759-4194, Nagato, JapanVascular malformations (VM) may become symptomatic and extensive, leading to deranged coagulation and bleeding. Sirolimus®, an antiangiogenic agent, has recently emerged as treatment for VM. We report its short-term outcomes for VMs of the extremities. Case 1: A 47-year-old female reported left forearm pain. MRI confirmed a VM. Lesion shrinkage and pain relief were not achieved despite sclerotherapy. After 5 months on Sirolimus®, improved pain, decreased forearm circumference and decreased lesion size on MRI were observed. Case 2: 62-year-old male reported left knee pain. MRI and biopsy confirmed a VM. After 3 months on Sirolimus®, improved pain, decreased leg circumference, and decreased lesion size on MRI were observed. Our series demonstrates that Sirolimus® is efficacious in downsizing VMs with resultant symptom relief in the short-term. Other series has likewise shown effectivity in extensive and refractory lesions, with benefits outweighing side effects.http://www.sciencedirect.com/science/article/pii/S1930043325002262RapamycinSirolimusVenous malformationUnresectableExtremity
spellingShingle Daniela Kristina Carolino, MD
Keiichi Muramatsu, MD
Yasuhiro Tani, MD
Hideaki Sugimoto, MD
Masaya Ueda, MD
The use of Sirolimus for an unresectable and refractory venous malformation: A case series
Radiology Case Reports
Rapamycin
Sirolimus
Venous malformation
Unresectable
Extremity
title The use of Sirolimus for an unresectable and refractory venous malformation: A case series
title_full The use of Sirolimus for an unresectable and refractory venous malformation: A case series
title_fullStr The use of Sirolimus for an unresectable and refractory venous malformation: A case series
title_full_unstemmed The use of Sirolimus for an unresectable and refractory venous malformation: A case series
title_short The use of Sirolimus for an unresectable and refractory venous malformation: A case series
title_sort use of sirolimus for an unresectable and refractory venous malformation a case series
topic Rapamycin
Sirolimus
Venous malformation
Unresectable
Extremity
url http://www.sciencedirect.com/science/article/pii/S1930043325002262
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