Criteria to define rare diseases and orphan drugs: a systematic review protocol
Introduction Rare diseases (RDs) are often chronic and progressive life-threatening medical conditions that affect a low percentage of the population compared with other diseases. These conditions can be treated with medications known as orphan drugs (ODs). Unfortunately, there is no universal defin...
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| Main Authors: | Katie Kerr, Ghada Mohammed Abozaid, Amy McKnight, Hussain A Al-Omar |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
BMJ Publishing Group
2022-07-01
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| Series: | BMJ Open |
| Online Access: | https://bmjopen.bmj.com/content/12/7/e062126.full |
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