Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report

<b>Background and Clinical Significance</b>: We report on an infant with Snijders Blok–Campeau syndrome (psychomotor developmental delay, CNS malformations) and a complex heart defect with pulmonary arterial hypertension. <b>Case Presentation</b>: A <i>DDX3X</i> m...

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Main Authors: Luisa Paul, Victoria C. Ziesenitz, Matthias Gorenflo
Format: Article
Language:English
Published: MDPI AG 2025-04-01
Series:Reports
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Online Access:https://www.mdpi.com/2571-841X/8/2/47
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author Luisa Paul
Victoria C. Ziesenitz
Matthias Gorenflo
author_facet Luisa Paul
Victoria C. Ziesenitz
Matthias Gorenflo
author_sort Luisa Paul
collection DOAJ
description <b>Background and Clinical Significance</b>: We report on an infant with Snijders Blok–Campeau syndrome (psychomotor developmental delay, CNS malformations) and a complex heart defect with pulmonary arterial hypertension. <b>Case Presentation</b>: A <i>DDX3X</i> mutation encoding for RNA helicase was detected, which may suggest an association between Snijders Blok–Campeau syndrome and the development of pulmonary vasculopathy. However, further validation is required. <b>Conclusions</b>: We suggest an important role for <i>DDX3X</i> in the development of the pulmonary vasculature.
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spelling doaj-art-2b4ecaef23f74617bf6c7ea69cbf1c232025-08-20T03:16:39ZengMDPI AGReports2571-841X2025-04-01824710.3390/reports8020047Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case ReportLuisa Paul0Victoria C. Ziesenitz1Matthias Gorenflo2Pediatric Cardiology and Congenital Heart Diseases, Centre for Child and Adolescent Medicine, University Hospital, Im Neuenheimer Feld, 430, 69120 Heidelberg, GermanyPediatric Cardiology and Congenital Heart Diseases, Centre for Child and Adolescent Medicine, University Hospital, Im Neuenheimer Feld, 430, 69120 Heidelberg, GermanyPediatric Cardiology and Congenital Heart Diseases, Centre for Child and Adolescent Medicine, University Hospital, Im Neuenheimer Feld, 430, 69120 Heidelberg, Germany<b>Background and Clinical Significance</b>: We report on an infant with Snijders Blok–Campeau syndrome (psychomotor developmental delay, CNS malformations) and a complex heart defect with pulmonary arterial hypertension. <b>Case Presentation</b>: A <i>DDX3X</i> mutation encoding for RNA helicase was detected, which may suggest an association between Snijders Blok–Campeau syndrome and the development of pulmonary vasculopathy. However, further validation is required. <b>Conclusions</b>: We suggest an important role for <i>DDX3X</i> in the development of the pulmonary vasculature.https://www.mdpi.com/2571-841X/8/2/47CHD3Snijders Blok–Campeau syndromecase reportvasculopathypulmonary arterial hypertension
spellingShingle Luisa Paul
Victoria C. Ziesenitz
Matthias Gorenflo
Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
Reports
CHD3
Snijders Blok–Campeau syndrome
case report
vasculopathy
pulmonary arterial hypertension
title Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
title_full Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
title_fullStr Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
title_full_unstemmed Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
title_short Snijders Blok–Campeau Syndrome Associated with Pulmonary Arterial Hypertension: A Case Report
title_sort snijders blok campeau syndrome associated with pulmonary arterial hypertension a case report
topic CHD3
Snijders Blok–Campeau syndrome
case report
vasculopathy
pulmonary arterial hypertension
url https://www.mdpi.com/2571-841X/8/2/47
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AT victoriacziesenitz snijdersblokcampeausyndromeassociatedwithpulmonaryarterialhypertensionacasereport
AT matthiasgorenflo snijdersblokcampeausyndromeassociatedwithpulmonaryarterialhypertensionacasereport