Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome

The 20S proteasome, a critical component of the ubiquitin–proteasome system, plays a central role in regulating protein degradation in eukaryotic cells. Marizomib (MZB), also known as salinosporamide A, is a natural γ-lactam-β-lactone compound derived from <i>Salinispora tropica</i> and...

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Main Authors: Hagen Sülzen, Pavla Fajtova, Anthony J. O’Donoghue, Jan Silhan, Evzen Boura
Format: Article
Language:English
Published: MDPI AG 2025-03-01
Series:Molecules
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Online Access:https://www.mdpi.com/1420-3049/30/6/1386
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author Hagen Sülzen
Pavla Fajtova
Anthony J. O’Donoghue
Jan Silhan
Evzen Boura
author_facet Hagen Sülzen
Pavla Fajtova
Anthony J. O’Donoghue
Jan Silhan
Evzen Boura
author_sort Hagen Sülzen
collection DOAJ
description The 20S proteasome, a critical component of the ubiquitin–proteasome system, plays a central role in regulating protein degradation in eukaryotic cells. Marizomib (MZB), also known as salinosporamide A, is a natural γ-lactam-β-lactone compound derived from <i>Salinispora tropica</i> and is a potent 20S proteasome covalent inhibitor with demonstrated anticancer properties. Its broad-spectrum inhibition of all three proteasome subunits and its ability to cross the blood–brain barrier has made it a promising therapeutic candidate for glioblastoma. In addition to this, MZB also demonstrates significant inhibition against the 20S proteasome of <i>Trichomonas vaginalis</i> (<i>Tv</i>20S), a protozoan parasite, suggesting its potential for parasitic treatments. Here, we present the cryo-EM structure of the human 20S proteasome in complex with MZB at 2.55 Å resolution. This structure reveals the binding mode of MZB to all six catalytic subunits within the two β-rings of the 20S proteasome, providing a detailed molecular understanding of its irreversible inhibitory mechanism. These findings enhance the therapeutic potential of MZB for both cancer and parasitic diseases at the molecular level and highlight marine-derived natural products in targeting the proteasome for therapeutic applications.
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spelling doaj-art-2a14da5f862c419ca260d09dc2b1beca2025-08-20T03:43:20ZengMDPI AGMolecules1420-30492025-03-01306138610.3390/molecules30061386Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S ProteasomeHagen Sülzen0Pavla Fajtova1Anthony J. O’Donoghue2Jan Silhan3Evzen Boura4Institute of Organic Chemistry and Biochemistry, Czech Academy of Sciences, Flemingovo namesti 2, 16610 Prague, Czech RepublicInstitute of Organic Chemistry and Biochemistry, Czech Academy of Sciences, Flemingovo namesti 2, 16610 Prague, Czech RepublicSkaggs School of Pharmacy and Pharmaceutical Sciences, University of California San Diego, La Jolla, CA 92093, USAInstitute of Organic Chemistry and Biochemistry, Czech Academy of Sciences, Flemingovo namesti 2, 16610 Prague, Czech RepublicInstitute of Organic Chemistry and Biochemistry, Czech Academy of Sciences, Flemingovo namesti 2, 16610 Prague, Czech RepublicThe 20S proteasome, a critical component of the ubiquitin–proteasome system, plays a central role in regulating protein degradation in eukaryotic cells. Marizomib (MZB), also known as salinosporamide A, is a natural γ-lactam-β-lactone compound derived from <i>Salinispora tropica</i> and is a potent 20S proteasome covalent inhibitor with demonstrated anticancer properties. Its broad-spectrum inhibition of all three proteasome subunits and its ability to cross the blood–brain barrier has made it a promising therapeutic candidate for glioblastoma. In addition to this, MZB also demonstrates significant inhibition against the 20S proteasome of <i>Trichomonas vaginalis</i> (<i>Tv</i>20S), a protozoan parasite, suggesting its potential for parasitic treatments. Here, we present the cryo-EM structure of the human 20S proteasome in complex with MZB at 2.55 Å resolution. This structure reveals the binding mode of MZB to all six catalytic subunits within the two β-rings of the 20S proteasome, providing a detailed molecular understanding of its irreversible inhibitory mechanism. These findings enhance the therapeutic potential of MZB for both cancer and parasitic diseases at the molecular level and highlight marine-derived natural products in targeting the proteasome for therapeutic applications.https://www.mdpi.com/1420-3049/30/6/138620SproteasomemarizomibMZBcryo-EM
spellingShingle Hagen Sülzen
Pavla Fajtova
Anthony J. O’Donoghue
Jan Silhan
Evzen Boura
Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
Molecules
20S
proteasome
marizomib
MZB
cryo-EM
title Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
title_full Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
title_fullStr Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
title_full_unstemmed Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
title_short Structural Insights into Salinosporamide a Mediated Inhibition of the Human 20S Proteasome
title_sort structural insights into salinosporamide a mediated inhibition of the human 20s proteasome
topic 20S
proteasome
marizomib
MZB
cryo-EM
url https://www.mdpi.com/1420-3049/30/6/1386
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AT anthonyjodonoghue structuralinsightsintosalinosporamideamediatedinhibitionofthehuman20sproteasome
AT jansilhan structuralinsightsintosalinosporamideamediatedinhibitionofthehuman20sproteasome
AT evzenboura structuralinsightsintosalinosporamideamediatedinhibitionofthehuman20sproteasome