Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study

Background Birt-Hogg-Dubé syndrome (BHD), a rare genetic disease characterized by multiple pulmonary cysts, can lead to spontaneous pneumothorax, cutaneous hamartomas, renal cysts, and renal cell cancer. The overall aim of this study was to assess clinical characteristics of patients with BHD-emphas...

Full description

Saved in:
Bibliographic Details
Main Authors: Marie Moldt Holmager, Sarah Wordenskjold Stougaard, Ole Graumann, Marianne Præstegaard, Lilian Bomme Ousager, Lars Lund, Annette Schuster, Casper Falster, Jesper Rømhild Davidsen
Format: Article
Language:English
Published: Taylor & Francis Group 2025-12-01
Series:European Clinical Respiratory Journal
Subjects:
Online Access:https://www.tandfonline.com/doi/10.1080/20018525.2024.2449271
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849716806647808000
author Marie Moldt Holmager
Sarah Wordenskjold Stougaard
Ole Graumann
Marianne Præstegaard
Lilian Bomme Ousager
Lars Lund
Annette Schuster
Casper Falster
Jesper Rømhild Davidsen
author_facet Marie Moldt Holmager
Sarah Wordenskjold Stougaard
Ole Graumann
Marianne Præstegaard
Lilian Bomme Ousager
Lars Lund
Annette Schuster
Casper Falster
Jesper Rømhild Davidsen
author_sort Marie Moldt Holmager
collection DOAJ
description Background Birt-Hogg-Dubé syndrome (BHD), a rare genetic disease characterized by multiple pulmonary cysts, can lead to spontaneous pneumothorax, cutaneous hamartomas, renal cysts, and renal cell cancer. The overall aim of this study was to assess clinical characteristics of patients with BHD-emphasizing on trends in pulmonary function patterns.Methods By use of data from electronic patient journals, we conducted a retrospective cohort study on clinical characteristics and pulmonary function tests (PFT) from patients with BHD, who were clinically followed-up in a Danish tertiary referral center for rare and interstitial lung diseases.Results A total of 101 patients (44 men (43.6%); mean age 48.4 years (SD ± 15.9 years)) with BHD were included. Chest HRCT scans revealed pulmonary cysts in 82.2% of whom 38.6% had experienced at least one pneumothorax (median 2; IQR1–4). Baseline PFT showed FEV1/FVC ratio and RV% within normal values of predicted. In 28.7% of the patients, a slight decrease in DLco below 80% of predicted was observed (mean 86.9% ± SD 15.8%). At two years follow-up, there were no significant declines in FEV1 and FVC, nor after accounting for age, gender, and smoking. At baseline cutaneous manifestations were found in 58.4% of the patients, 47.5% had benign renal cysts, and 11.9% had renal tumours.Conclusion More than 80% of patients with BHD presented with pulmonary cysts, but consistent with other studies all had normal PFTs at two years follow-up. We conclude that routine monitoring of pulmonary function and pulmonary follow-up may not be necessary in patients with BHD.
format Article
id doaj-art-24dbdf05d0a747dbbd5057b28347a983
institution DOAJ
issn 2001-8525
language English
publishDate 2025-12-01
publisher Taylor & Francis Group
record_format Article
series European Clinical Respiratory Journal
spelling doaj-art-24dbdf05d0a747dbbd5057b28347a9832025-08-20T03:12:51ZengTaylor & Francis GroupEuropean Clinical Respiratory Journal2001-85252025-12-0112110.1080/20018525.2024.2449271Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort studyMarie Moldt Holmager0Sarah Wordenskjold Stougaard1Ole Graumann2Marianne Præstegaard3Lilian Bomme Ousager4Lars Lund5Annette Schuster6Casper Falster7Jesper Rømhild Davidsen8Department of Respiratory Medicine, Odense University Hospital, Odense, DenmarkRadiological Research and Innovation Unit (UNIFY), Department of Clinical Research, University of Southern Denmark, Odense, DenmarkRadiological Research and Innovation Unit (UNIFY), Department of Clinical Research, University of Southern Denmark, Odense, DenmarkCenter for Complex and Rare Diseases, Department of Clinical Genetics, Odense University Hospital, Odense, DenmarkCenter for Complex and Rare Diseases, Department of Clinical Genetics, Odense University Hospital, Odense, DenmarkDepartment of Clinical Research, University of Southern Denmark, Odense, DenmarkDepartment of Dermatology and Allergy Centre, Odense University Hospital, Odense, DenmarkDepartment of Respiratory Medicine, Odense University Hospital, Odense, DenmarkDepartment of Respiratory Medicine, Odense University Hospital, Odense, DenmarkBackground Birt-Hogg-Dubé syndrome (BHD), a rare genetic disease characterized by multiple pulmonary cysts, can lead to spontaneous pneumothorax, cutaneous hamartomas, renal cysts, and renal cell cancer. The overall aim of this study was to assess clinical characteristics of patients with BHD-emphasizing on trends in pulmonary function patterns.Methods By use of data from electronic patient journals, we conducted a retrospective cohort study on clinical characteristics and pulmonary function tests (PFT) from patients with BHD, who were clinically followed-up in a Danish tertiary referral center for rare and interstitial lung diseases.Results A total of 101 patients (44 men (43.6%); mean age 48.4 years (SD ± 15.9 years)) with BHD were included. Chest HRCT scans revealed pulmonary cysts in 82.2% of whom 38.6% had experienced at least one pneumothorax (median 2; IQR1–4). Baseline PFT showed FEV1/FVC ratio and RV% within normal values of predicted. In 28.7% of the patients, a slight decrease in DLco below 80% of predicted was observed (mean 86.9% ± SD 15.8%). At two years follow-up, there were no significant declines in FEV1 and FVC, nor after accounting for age, gender, and smoking. At baseline cutaneous manifestations were found in 58.4% of the patients, 47.5% had benign renal cysts, and 11.9% had renal tumours.Conclusion More than 80% of patients with BHD presented with pulmonary cysts, but consistent with other studies all had normal PFTs at two years follow-up. We conclude that routine monitoring of pulmonary function and pulmonary follow-up may not be necessary in patients with BHD.https://www.tandfonline.com/doi/10.1080/20018525.2024.2449271Birt-Hogg-Dubé syndromeorphan pulmonary diseasespulmonary function testdiffuse interstitial lung diseasecohort study
spellingShingle Marie Moldt Holmager
Sarah Wordenskjold Stougaard
Ole Graumann
Marianne Præstegaard
Lilian Bomme Ousager
Lars Lund
Annette Schuster
Casper Falster
Jesper Rømhild Davidsen
Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
European Clinical Respiratory Journal
Birt-Hogg-Dubé syndrome
orphan pulmonary diseases
pulmonary function test
diffuse interstitial lung disease
cohort study
title Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
title_full Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
title_fullStr Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
title_full_unstemmed Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
title_short Trends in pulmonary function in patients with Birt-Hogg-Dubé syndrome: a retrospective cohort study
title_sort trends in pulmonary function in patients with birt hogg dube syndrome a retrospective cohort study
topic Birt-Hogg-Dubé syndrome
orphan pulmonary diseases
pulmonary function test
diffuse interstitial lung disease
cohort study
url https://www.tandfonline.com/doi/10.1080/20018525.2024.2449271
work_keys_str_mv AT mariemoldtholmager trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT sarahwordenskjoldstougaard trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT olegraumann trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT mariannepræstegaard trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT lilianbommeousager trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT larslund trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT annetteschuster trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT casperfalster trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy
AT jesperrømhilddavidsen trendsinpulmonaryfunctioninpatientswithbirthoggdubesyndromearetrospectivecohortstudy