Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy

Complement C5 inhibitors bring an increased risk for Neisseria infections. A novel complement C3 inhibitor, pegcetacoplan, was recently approved to treat paroxysmal nocturnal hemoglobinuria, a condition commonly treated with complement C5 inhibitors. We present a case of meningococcal sepsis in a p...

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Main Authors: Leo Starck, Vuokko Nummi, Eira Poikonen, Anna-Elina Lehtinen, Pia Kivelä, Nathalie Friberg, Jukka Torvikoski, Maija Toropainen, Seppo Meri
Format: Article
Language:English
Published: Centers for Disease Control and Prevention 2025-03-01
Series:Emerging Infectious Diseases
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Online Access:https://wwwnc.cdc.gov/eid/article/31/3/24-1182_article
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author Leo Starck
Vuokko Nummi
Eira Poikonen
Anna-Elina Lehtinen
Pia Kivelä
Nathalie Friberg
Jukka Torvikoski
Maija Toropainen
Seppo Meri
author_facet Leo Starck
Vuokko Nummi
Eira Poikonen
Anna-Elina Lehtinen
Pia Kivelä
Nathalie Friberg
Jukka Torvikoski
Maija Toropainen
Seppo Meri
author_sort Leo Starck
collection DOAJ
description Complement C5 inhibitors bring an increased risk for Neisseria infections. A novel complement C3 inhibitor, pegcetacoplan, was recently approved to treat paroxysmal nocturnal hemoglobinuria, a condition commonly treated with complement C5 inhibitors. We present a case of meningococcal sepsis in a pegcetacoplan-treated patient with aplastic anemia and paroxysmal nocturnal hemoglobinuria.
format Article
id doaj-art-23d863dfebc74c4e996f1449d47fdf5c
institution DOAJ
issn 1080-6040
1080-6059
language English
publishDate 2025-03-01
publisher Centers for Disease Control and Prevention
record_format Article
series Emerging Infectious Diseases
spelling doaj-art-23d863dfebc74c4e996f1449d47fdf5c2025-08-20T03:00:03ZengCenters for Disease Control and PreventionEmerging Infectious Diseases1080-60401080-60592025-03-0131358358610.3201/eid3103.241182Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan TherapyLeo StarckVuokko NummiEira PoikonenAnna-Elina LehtinenPia KiveläNathalie FribergJukka TorvikoskiMaija ToropainenSeppo Meri Complement C5 inhibitors bring an increased risk for Neisseria infections. A novel complement C3 inhibitor, pegcetacoplan, was recently approved to treat paroxysmal nocturnal hemoglobinuria, a condition commonly treated with complement C5 inhibitors. We present a case of meningococcal sepsis in a pegcetacoplan-treated patient with aplastic anemia and paroxysmal nocturnal hemoglobinuria. https://wwwnc.cdc.gov/eid/article/31/3/24-1182_articleMeningococcalsepsisparoxysmal nocturnal hemoglobinuriapegcetacoplanNeisseria meningitidiscomplement
spellingShingle Leo Starck
Vuokko Nummi
Eira Poikonen
Anna-Elina Lehtinen
Pia Kivelä
Nathalie Friberg
Jukka Torvikoski
Maija Toropainen
Seppo Meri
Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
Emerging Infectious Diseases
Meningococcal
sepsis
paroxysmal nocturnal hemoglobinuria
pegcetacoplan
Neisseria meningitidis
complement
title Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
title_full Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
title_fullStr Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
title_full_unstemmed Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
title_short Meningococcal Sepsis in Patient with Paroxysmal Nocturnal Hemoglobinuria during Pegcetacoplan Therapy
title_sort meningococcal sepsis in patient with paroxysmal nocturnal hemoglobinuria during pegcetacoplan therapy
topic Meningococcal
sepsis
paroxysmal nocturnal hemoglobinuria
pegcetacoplan
Neisseria meningitidis
complement
url https://wwwnc.cdc.gov/eid/article/31/3/24-1182_article
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