P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence

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Main Authors: Erin Prange, Shannon Standridge, Constance Smith-Hicks, Jennifer Tu, Davut Pehlivan, Steven Skinner, Cary Fu, Stephanie Kyle, Alyssa Peckham
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425003310
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author Erin Prange
Shannon Standridge
Constance Smith-Hicks
Jennifer Tu
Davut Pehlivan
Steven Skinner
Cary Fu
Stephanie Kyle
Alyssa Peckham
author_facet Erin Prange
Shannon Standridge
Constance Smith-Hicks
Jennifer Tu
Davut Pehlivan
Steven Skinner
Cary Fu
Stephanie Kyle
Alyssa Peckham
author_sort Erin Prange
collection DOAJ
format Article
id doaj-art-2334cbc0708d49919d30fc0c08d3f8b8
institution OA Journals
issn 2949-7744
language English
publishDate 2025-01-01
publisher Elsevier
record_format Article
series Genetics in Medicine Open
spelling doaj-art-2334cbc0708d49919d30fc0c08d3f8b82025-08-20T02:18:47ZengElsevierGenetics in Medicine Open2949-77442025-01-01310229210.1016/j.gimo.2025.102292P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellenceErin Prange0Shannon Standridge1Constance Smith-Hicks2Jennifer Tu3Davut Pehlivan4Steven Skinner5Cary Fu6Stephanie Kyle7Alyssa Peckham8Children's Hospital of Philadelphia, Philadelphia, PAUniversity of Cincinnati School of Medicine, Cincinnati Children's Hospital Medical Center, Cincinnati, OHCenter for Synaptic Disorders, Rett and Related Disorders Clinic, Kennedy Krieger Institute, MDUniversity of California San Francisco Benioff Children's Hospital, Oakland, CABaylor College of Medicine, Houston, TXGreenwood Genetic Center, Greenwood, SCVanderbilt Kennedy Center, Vanderbilt University Medical Center, Nashville, TNAcadia Pharmaceuticals Inc., San Diego, CAAcadia Pharmaceuticals Inc., San Diego, CAhttp://www.sciencedirect.com/science/article/pii/S2949774425003310
spellingShingle Erin Prange
Shannon Standridge
Constance Smith-Hicks
Jennifer Tu
Davut Pehlivan
Steven Skinner
Cary Fu
Stephanie Kyle
Alyssa Peckham
P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
Genetics in Medicine Open
title P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
title_full P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
title_fullStr P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
title_full_unstemmed P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
title_short P327: Real-world use of trofinetide: A survey of tolerability from US Rett syndrome centers of excellence
title_sort p327 real world use of trofinetide a survey of tolerability from us rett syndrome centers of excellence
url http://www.sciencedirect.com/science/article/pii/S2949774425003310
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