Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis

Abstract Prostate cancer (PCa) diagnosis remains challenging due to overlapping clinical features with benign prostatic hyperplasia (BPH) and limitations of existing diagnostic tools like PSA tests, which yield high false-positive rates. This study investigates the potential of microRNA (miRNA) biom...

Full description

Saved in:
Bibliographic Details
Main Authors: Shweta Singh, Abhay Kumar Pathak, Sukhad Kural, Lalit Kumar, Madan Gopal Bhardwaj, Mahima Yadav, Sameer Trivedi, Parimal Das, Manjari Gupta, Garima Jain
Format: Article
Language:English
Published: Nature Portfolio 2025-08-01
Series:Scientific Reports
Subjects:
Online Access:https://doi.org/10.1038/s41598-025-99754-7
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849226407432945664
author Shweta Singh
Abhay Kumar Pathak
Sukhad Kural
Lalit Kumar
Madan Gopal Bhardwaj
Mahima Yadav
Sameer Trivedi
Parimal Das
Manjari Gupta
Garima Jain
author_facet Shweta Singh
Abhay Kumar Pathak
Sukhad Kural
Lalit Kumar
Madan Gopal Bhardwaj
Mahima Yadav
Sameer Trivedi
Parimal Das
Manjari Gupta
Garima Jain
author_sort Shweta Singh
collection DOAJ
description Abstract Prostate cancer (PCa) diagnosis remains challenging due to overlapping clinical features with benign prostatic hyperplasia (BPH) and limitations of existing diagnostic tools like PSA tests, which yield high false-positive rates. This study investigates the potential of microRNA (miRNA) biomarkers, analyzed via reverse transcription polymerase chain reaction and machine learning (ML), to enhance diagnostic accuracy. miRNAs such as miR-21-5p, miR-141-3p, and miR-221-3p were identified as significant discriminators between PCa and BPH through a prospective cohort study. Whole blood miRNA profiling offered a robust systemic representation of disease states. A random forest ML model was trained on expression data, achieving notable performance metrics: an accuracy of 77.42%, AUC of 0.78 during verification, and 74.07% accuracy and 0.75 AUC in validation. The model’s use of miRNA expression ratios, such as miR-141-3p/miR-221-3p, demonstrated superior sensitivity and specificity over traditional PSA testing. Bioinformatics analysis confirmed the association of selected miRNAs with cancer pathways, including PD-L1/PD-1 checkpoint and androgen receptor signaling, validating the biological relevance of the findings. This novel integration of miRNA profiling and machine learning holds great potential for the clinical translation of miRNA-based non-invasive diagnostics, enhancing diagnostic precision. However, broader population studies and standardization of protocols are needed to ensure scalability and clinical applicability. This research provides a foundational framework for advancing miRNA-based diagnostics, bridging discovery and clinical implementation.
format Article
id doaj-art-1fae9430a67b454e8415b5ce7b77df0a
institution Kabale University
issn 2045-2322
language English
publishDate 2025-08-01
publisher Nature Portfolio
record_format Article
series Scientific Reports
spelling doaj-art-1fae9430a67b454e8415b5ce7b77df0a2025-08-24T11:21:11ZengNature PortfolioScientific Reports2045-23222025-08-0115111210.1038/s41598-025-99754-7Integrating miRNA profiling and machine learning for improved prostate cancer diagnosisShweta Singh0Abhay Kumar Pathak1Sukhad Kural2Lalit Kumar3Madan Gopal Bhardwaj4Mahima Yadav5Sameer Trivedi6Parimal Das7Manjari Gupta8Garima Jain9MIRNOW, BIONEST, Banaras Hindu UniversityDST-CIMS, Institute of Science, Banaras Hindu UniversityDepartment of Urology, Institute of Medical Sciences, Banaras Hindu UniversityDepartment of Urology, Institute of Medical Sciences, Banaras Hindu UniversityDepartment of Urology, Institute of Medical Sciences, Banaras Hindu UniversityDepartment of Pathology, Institute of Medical Sciences, Banaras Hindu UniversityDepartment of Urology, Institute of Medical Sciences, Banaras Hindu UniversityCentre for Genetic Disorders, Institute of Science, Banaras Hindu UniversityDST-CIMS, Institute of Science, Banaras Hindu UniversityCentre for Genetic Disorders, Institute of Science, Banaras Hindu UniversityAbstract Prostate cancer (PCa) diagnosis remains challenging due to overlapping clinical features with benign prostatic hyperplasia (BPH) and limitations of existing diagnostic tools like PSA tests, which yield high false-positive rates. This study investigates the potential of microRNA (miRNA) biomarkers, analyzed via reverse transcription polymerase chain reaction and machine learning (ML), to enhance diagnostic accuracy. miRNAs such as miR-21-5p, miR-141-3p, and miR-221-3p were identified as significant discriminators between PCa and BPH through a prospective cohort study. Whole blood miRNA profiling offered a robust systemic representation of disease states. A random forest ML model was trained on expression data, achieving notable performance metrics: an accuracy of 77.42%, AUC of 0.78 during verification, and 74.07% accuracy and 0.75 AUC in validation. The model’s use of miRNA expression ratios, such as miR-141-3p/miR-221-3p, demonstrated superior sensitivity and specificity over traditional PSA testing. Bioinformatics analysis confirmed the association of selected miRNAs with cancer pathways, including PD-L1/PD-1 checkpoint and androgen receptor signaling, validating the biological relevance of the findings. This novel integration of miRNA profiling and machine learning holds great potential for the clinical translation of miRNA-based non-invasive diagnostics, enhancing diagnostic precision. However, broader population studies and standardization of protocols are needed to ensure scalability and clinical applicability. This research provides a foundational framework for advancing miRNA-based diagnostics, bridging discovery and clinical implementation.https://doi.org/10.1038/s41598-025-99754-7Liquid biopsyRandom forestProstate cancermiRNAsBiomarkerCancer diagnostics
spellingShingle Shweta Singh
Abhay Kumar Pathak
Sukhad Kural
Lalit Kumar
Madan Gopal Bhardwaj
Mahima Yadav
Sameer Trivedi
Parimal Das
Manjari Gupta
Garima Jain
Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
Scientific Reports
Liquid biopsy
Random forest
Prostate cancer
miRNAs
Biomarker
Cancer diagnostics
title Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
title_full Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
title_fullStr Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
title_full_unstemmed Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
title_short Integrating miRNA profiling and machine learning for improved prostate cancer diagnosis
title_sort integrating mirna profiling and machine learning for improved prostate cancer diagnosis
topic Liquid biopsy
Random forest
Prostate cancer
miRNAs
Biomarker
Cancer diagnostics
url https://doi.org/10.1038/s41598-025-99754-7
work_keys_str_mv AT shwetasingh integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT abhaykumarpathak integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT sukhadkural integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT lalitkumar integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT madangopalbhardwaj integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT mahimayadav integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT sameertrivedi integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT parimaldas integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT manjarigupta integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis
AT garimajain integratingmirnaprofilingandmachinelearningforimprovedprostatecancerdiagnosis