Nonclinical evaluation of HBG1/2 and BCL11A as genome-editing targets for the treatment of β-hemoglobinopathies

Nonclinical evaluation of HBG1/2 and BCL11A as genome-editing targets for the treatment of β-hemoglobinopathies

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Bibliographic Details
Main Authors:	Tusneem Janoudi, Mrunali Jagdale, Meng Wu, Sanjana Gorlla, Peisheng Zhang, Ying Shao, Li Li, Sheryl R. Bowley, Eugenio Marco, Kai-Hsin Chang
Format:	Article
Language:	English
Published:	Elsevier 2025-02-01
Series:	Blood Advances
Online Access:	http://www.sciencedirect.com/science/article/pii/S2473952924007055
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