Generation and purification of iPSC-derived cardiomyocytes for clinical applications

Abstract Background Over the past decade, the field of cell therapy has rapidly expanded with the aim to replace and repair damaged cells and/or tissue. Depending on the disease many different cell types can be used as part of such a therapy. Here we focused on the potential treatment of myocardial...

Full description

Saved in:
Bibliographic Details
Main Authors: M. Generali, D. Kehl, D. Meier, D. Zorndt, K. Atrott, H. Saito, MY. Emmert, SP. Hoerstrup
Format: Article
Language:English
Published: BMC 2025-04-01
Series:Stem Cell Research & Therapy
Subjects:
Online Access:https://doi.org/10.1186/s13287-025-04319-0
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850182024874164224
author M. Generali
D. Kehl
D. Meier
D. Zorndt
K. Atrott
H. Saito
MY. Emmert
SP. Hoerstrup
author_facet M. Generali
D. Kehl
D. Meier
D. Zorndt
K. Atrott
H. Saito
MY. Emmert
SP. Hoerstrup
author_sort M. Generali
collection DOAJ
description Abstract Background Over the past decade, the field of cell therapy has rapidly expanded with the aim to replace and repair damaged cells and/or tissue. Depending on the disease many different cell types can be used as part of such a therapy. Here we focused on the potential treatment of myocardial infarction, where currently available treatment options are not able to regenerate the loss of healthy heart tissue. Method We generated good manufacturing practice (GMP)-compatible cardiomyocytes (iCMs) from transgene- and xenofree induced pluripotent stem cells (iPSCs) that can be seamless adapted for clinical applications. Further protocols were established for replating and freezing/thawing iCMs under xenofree conditions. Results iCMs showed a cardiac phenotype, with the expression of specific cardiac markers and absence of pluripotency markers at RNA and protein level. To ensure a pure iCMs population for in vivo applications, we minimized risks of iPSC contamination using RNA-switch technology to ensure safety. Conclusion We describe the generation and further processing of xeno- and transgene-free iCMs. The use of GMP-compliant differentiation protocols ab initio facilitates the clinical translation of this project in later stages.
format Article
id doaj-art-1866aaf9ce414ae9b012da804c853e44
institution OA Journals
issn 1757-6512
language English
publishDate 2025-04-01
publisher BMC
record_format Article
series Stem Cell Research & Therapy
spelling doaj-art-1866aaf9ce414ae9b012da804c853e442025-08-20T02:17:46ZengBMCStem Cell Research & Therapy1757-65122025-04-0116111210.1186/s13287-025-04319-0Generation and purification of iPSC-derived cardiomyocytes for clinical applicationsM. Generali0D. Kehl1D. Meier2D. Zorndt3K. Atrott4H. Saito5MY. Emmert6SP. Hoerstrup7Institute for Regenerative Medicine, University of ZurichInstitute for Regenerative Medicine, University of ZurichInstitute for Regenerative Medicine, University of ZurichInstitute for Regenerative Medicine, University of ZurichCenter for Surgical Research, University of Zurich, University Hospital ZurichDepartment of Life Science Frontiers, Center for iPS Cell Research and Application, Kyoto UniversityInstitute for Regenerative Medicine, University of ZurichInstitute for Regenerative Medicine, University of ZurichAbstract Background Over the past decade, the field of cell therapy has rapidly expanded with the aim to replace and repair damaged cells and/or tissue. Depending on the disease many different cell types can be used as part of such a therapy. Here we focused on the potential treatment of myocardial infarction, where currently available treatment options are not able to regenerate the loss of healthy heart tissue. Method We generated good manufacturing practice (GMP)-compatible cardiomyocytes (iCMs) from transgene- and xenofree induced pluripotent stem cells (iPSCs) that can be seamless adapted for clinical applications. Further protocols were established for replating and freezing/thawing iCMs under xenofree conditions. Results iCMs showed a cardiac phenotype, with the expression of specific cardiac markers and absence of pluripotency markers at RNA and protein level. To ensure a pure iCMs population for in vivo applications, we minimized risks of iPSC contamination using RNA-switch technology to ensure safety. Conclusion We describe the generation and further processing of xeno- and transgene-free iCMs. The use of GMP-compliant differentiation protocols ab initio facilitates the clinical translation of this project in later stages.https://doi.org/10.1186/s13287-025-04319-0Induced pluripotent stem cellsCardiomyocytesCell therapyClinical translation
spellingShingle M. Generali
D. Kehl
D. Meier
D. Zorndt
K. Atrott
H. Saito
MY. Emmert
SP. Hoerstrup
Generation and purification of iPSC-derived cardiomyocytes for clinical applications
Stem Cell Research & Therapy
Induced pluripotent stem cells
Cardiomyocytes
Cell therapy
Clinical translation
title Generation and purification of iPSC-derived cardiomyocytes for clinical applications
title_full Generation and purification of iPSC-derived cardiomyocytes for clinical applications
title_fullStr Generation and purification of iPSC-derived cardiomyocytes for clinical applications
title_full_unstemmed Generation and purification of iPSC-derived cardiomyocytes for clinical applications
title_short Generation and purification of iPSC-derived cardiomyocytes for clinical applications
title_sort generation and purification of ipsc derived cardiomyocytes for clinical applications
topic Induced pluripotent stem cells
Cardiomyocytes
Cell therapy
Clinical translation
url https://doi.org/10.1186/s13287-025-04319-0
work_keys_str_mv AT mgenerali generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT dkehl generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT dmeier generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT dzorndt generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT katrott generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT hsaito generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT myemmert generationandpurificationofipscderivedcardiomyocytesforclinicalapplications
AT sphoerstrup generationandpurificationofipscderivedcardiomyocytesforclinicalapplications