Inhibition of Cbl-b restores effector functions of human intratumoral NK cells

Background T cell-based immunotherapies including immune checkpoint blockade and chimeric antigen receptor T cells can induce durable responses in patients with cancer. However, clinical efficacy is limited due to the ability of cancer cells to evade immune surveillance. While T cells have been the...

Full description

Saved in:
Bibliographic Details
Main Authors: Alfred Zippelius, Mélanie Buchi, Petra Herzig, Heinz Läubli, Kirsten D Mertz, Viola Heinzelmann-Schwarz, Didier Lardinois, Marina Natoli, Clara Serger, Alberto Toso, Nicole Brodmann, Sofia Tundo, Marcel Trefny, Andrijana Rodić, Olivia Grueninger, Anastasiya Börsch, Jonas Fürst, Katarzyna Buczak, Alex T Müller, Lisa Sach-Peltason, Leyla Don, Aljaž Hojski, Karin Schaeuble, Thuy T Luu, Andrea Romagnani
Format: Article
Language:English
Published: BMJ Publishing Group 2024-11-01
Series:Journal for ImmunoTherapy of Cancer
Online Access:https://jitc.bmj.com/content/12/11/e009860.full
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849309637699960832
author Alfred Zippelius
Mélanie Buchi
Petra Herzig
Heinz Läubli
Kirsten D Mertz
Viola Heinzelmann-Schwarz
Didier Lardinois
Marina Natoli
Clara Serger
Alberto Toso
Nicole Brodmann
Sofia Tundo
Marcel Trefny
Andrijana Rodić
Olivia Grueninger
Anastasiya Börsch
Jonas Fürst
Katarzyna Buczak
Alex T Müller
Lisa Sach-Peltason
Leyla Don
Aljaž Hojski
Karin Schaeuble
Thuy T Luu
Andrea Romagnani
author_facet Alfred Zippelius
Mélanie Buchi
Petra Herzig
Heinz Läubli
Kirsten D Mertz
Viola Heinzelmann-Schwarz
Didier Lardinois
Marina Natoli
Clara Serger
Alberto Toso
Nicole Brodmann
Sofia Tundo
Marcel Trefny
Andrijana Rodić
Olivia Grueninger
Anastasiya Börsch
Jonas Fürst
Katarzyna Buczak
Alex T Müller
Lisa Sach-Peltason
Leyla Don
Aljaž Hojski
Karin Schaeuble
Thuy T Luu
Andrea Romagnani
author_sort Alfred Zippelius
collection DOAJ
description Background T cell-based immunotherapies including immune checkpoint blockade and chimeric antigen receptor T cells can induce durable responses in patients with cancer. However, clinical efficacy is limited due to the ability of cancer cells to evade immune surveillance. While T cells have been the primary focus of immunotherapy, recent research has highlighted the importance of natural killer (NK) cells in directly recognizing and eliminating tumor cells and playing a key role in the set-up of an effective adaptive immune response. The remarkable potential of NK cells for cancer immunotherapy is demonstrated by their ability to broadly identify stressed cells, irrespective of the presence of neoantigens, and their ability to fight tumors that have lost their major histocompatibility complex class I (MHC I) expression due to acquired resistance mechanisms.However, like T cells, NK cells can become dysfunctional within the tumor microenvironment. Strategies to enhance and reinvigorate NK cell activity hold potential for bolstering cancer immunotherapy.Methods In this study, we conducted a high-throughput screen to identify molecules that could enhance primary human NK cell function. After compound validation, we investigated the effect of the top performing compounds on dysfunctional NK cells that were generated by a newly developed in vitro platform. Functional activity of NK cells was investigated using compounds alone and in combination with checkpoint inhibitor blockade. The findings were validated on patient-derived intratumoral dysfunctional NK cells from different cancer types.Results The screening approach led to the identification of a Casitas B-lineage lymphoma (Cbl-b) inhibitor enhancing the activity of primary human NK cells. Furthermore, the Cbl-b inhibitor was able to reinvigorate the activity of in vitro generated and patient-derived dysfunctional NK cells. Finally, Cbl-b inhibition combined with T-cell immunoreceptor with Ig and ITIM domains (TIGIT) blockade further increased the cytotoxic potential and reinvigoration of both in vitro generated and patient-derived intratumoral dysfunctional NK cells.Conclusions These findings underscore the relevance of Cbl-b inhibition in overcoming NK cell dysfunctionality with the potential to complement existing immunotherapies and improve outcomes for patients with cancer.
format Article
id doaj-art-0bded18942fa48e2a0fc5413e4d9249a
institution Kabale University
issn 2051-1426
language English
publishDate 2024-11-01
publisher BMJ Publishing Group
record_format Article
series Journal for ImmunoTherapy of Cancer
spelling doaj-art-0bded18942fa48e2a0fc5413e4d9249a2025-08-20T03:54:01ZengBMJ Publishing GroupJournal for ImmunoTherapy of Cancer2051-14262024-11-01121110.1136/jitc-2024-009860Inhibition of Cbl-b restores effector functions of human intratumoral NK cellsAlfred Zippelius0Mélanie Buchi1Petra Herzig2Heinz Läubli3Kirsten D Mertz4Viola Heinzelmann-Schwarz5Didier Lardinois6Marina Natoli7Clara Serger8Alberto Toso9Nicole Brodmann10Sofia Tundo11Marcel Trefny12Andrijana Rodić13Olivia Grueninger14Anastasiya Börsch15Jonas Fürst16Katarzyna Buczak17Alex T Müller18Lisa Sach-Peltason19Leyla Don20Aljaž Hojski21Karin Schaeuble22Thuy T Luu23Andrea Romagnani249 Medical Oncology, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland9 Medical Oncology, University Hospital Basel, Basel, Switzerland8 Institute of Pathology, Cantonal Hospital Basel-Landschaft, Liestal, Switzerland7 Department of Gynecology and Obstetrics, University Hospital Basel, Basel, Switzerland6 Department of Thoracic Surgery, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, Switzerland3 Department of Biomedicine, Bioinformatics Core Facility, University of Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland5 Biozentrum, Proteomics Core Facility, University of Basel, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland6 Department of Thoracic Surgery, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland1 Department of Biomedicine, University Hospital Basel, Basel, Switzerland2 Roche Innovation Center, F. Hoffmann-La Roche AG, Roche Pharma Research and Early Development, Basel, SwitzerlandBackground T cell-based immunotherapies including immune checkpoint blockade and chimeric antigen receptor T cells can induce durable responses in patients with cancer. However, clinical efficacy is limited due to the ability of cancer cells to evade immune surveillance. While T cells have been the primary focus of immunotherapy, recent research has highlighted the importance of natural killer (NK) cells in directly recognizing and eliminating tumor cells and playing a key role in the set-up of an effective adaptive immune response. The remarkable potential of NK cells for cancer immunotherapy is demonstrated by their ability to broadly identify stressed cells, irrespective of the presence of neoantigens, and their ability to fight tumors that have lost their major histocompatibility complex class I (MHC I) expression due to acquired resistance mechanisms.However, like T cells, NK cells can become dysfunctional within the tumor microenvironment. Strategies to enhance and reinvigorate NK cell activity hold potential for bolstering cancer immunotherapy.Methods In this study, we conducted a high-throughput screen to identify molecules that could enhance primary human NK cell function. After compound validation, we investigated the effect of the top performing compounds on dysfunctional NK cells that were generated by a newly developed in vitro platform. Functional activity of NK cells was investigated using compounds alone and in combination with checkpoint inhibitor blockade. The findings were validated on patient-derived intratumoral dysfunctional NK cells from different cancer types.Results The screening approach led to the identification of a Casitas B-lineage lymphoma (Cbl-b) inhibitor enhancing the activity of primary human NK cells. Furthermore, the Cbl-b inhibitor was able to reinvigorate the activity of in vitro generated and patient-derived dysfunctional NK cells. Finally, Cbl-b inhibition combined with T-cell immunoreceptor with Ig and ITIM domains (TIGIT) blockade further increased the cytotoxic potential and reinvigoration of both in vitro generated and patient-derived intratumoral dysfunctional NK cells.Conclusions These findings underscore the relevance of Cbl-b inhibition in overcoming NK cell dysfunctionality with the potential to complement existing immunotherapies and improve outcomes for patients with cancer.https://jitc.bmj.com/content/12/11/e009860.full
spellingShingle Alfred Zippelius
Mélanie Buchi
Petra Herzig
Heinz Läubli
Kirsten D Mertz
Viola Heinzelmann-Schwarz
Didier Lardinois
Marina Natoli
Clara Serger
Alberto Toso
Nicole Brodmann
Sofia Tundo
Marcel Trefny
Andrijana Rodić
Olivia Grueninger
Anastasiya Börsch
Jonas Fürst
Katarzyna Buczak
Alex T Müller
Lisa Sach-Peltason
Leyla Don
Aljaž Hojski
Karin Schaeuble
Thuy T Luu
Andrea Romagnani
Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
Journal for ImmunoTherapy of Cancer
title Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
title_full Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
title_fullStr Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
title_full_unstemmed Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
title_short Inhibition of Cbl-b restores effector functions of human intratumoral NK cells
title_sort inhibition of cbl b restores effector functions of human intratumoral nk cells
url https://jitc.bmj.com/content/12/11/e009860.full
work_keys_str_mv AT alfredzippelius inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT melaniebuchi inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT petraherzig inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT heinzlaubli inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT kirstendmertz inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT violaheinzelmannschwarz inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT didierlardinois inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT marinanatoli inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT claraserger inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT albertotoso inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT nicolebrodmann inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT sofiatundo inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT marceltrefny inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT andrijanarodic inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT oliviagrueninger inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT anastasiyaborsch inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT jonasfurst inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT katarzynabuczak inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT alextmuller inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT lisasachpeltason inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT leyladon inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT aljazhojski inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT karinschaeuble inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT thuytluu inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells
AT andrearomagnani inhibitionofcblbrestoreseffectorfunctionsofhumanintratumoralnkcells