A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden

OBJECTIVES: This research aimed to provide updated epidemiological estimates of multiple myeloma (MM) in Italy and to characterize the clinical journey, treatment patterns, and economic burden focusing specifically on the subset of patients who have been exposed to all three major therapeutic classe...

Full description

Saved in:
Bibliographic Details
Main Authors: Valentina Perrone, Stefania Mazzoni, Maria Cappuccilli, Roberto Di Virgilio, Luca Degli Esposti
Format: Article
Language:English
Published: SEEd Medical Publishers 2025-07-01
Series:Farmeconomia: Health Economics and Therapeutic Pathways
Subjects:
Online Access:https://journals.seedmedicalpublishers.com/index.php/FE/article/view/1580
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850082891977981952
author Valentina Perrone
Stefania Mazzoni
Maria Cappuccilli
Roberto Di Virgilio
Luca Degli Esposti
author_facet Valentina Perrone
Stefania Mazzoni
Maria Cappuccilli
Roberto Di Virgilio
Luca Degli Esposti
author_sort Valentina Perrone
collection DOAJ
description OBJECTIVES: This research aimed to provide updated epidemiological estimates of multiple myeloma (MM) in Italy and to characterize the clinical journey, treatment patterns, and economic burden focusing specifically on the subset of patients who have been exposed to all three major therapeutic classes: proteasome inhibitors, immunomodulatory drugs, and antiCD38 monoclonal antibodies (triple-class exposed, TCE). METHODS: A retrospective analysis was conducted using Italian healthcare administrative databases covering 12 million individuals. The research included (i) an epidemiological analysis of MM prevalence and incidence, and (ii) a longitudinal analysis of TCE patients identified between January 2017 and June 2023. Inclusion criteria required exposure to the three major MM drug classes. Healthcare resource utilization (HCRU) and direct costs from the Italian National Health Service perspective were assessed at one-year follow-up. RESULTS: As of August 2022, MM incidence was 9/100,000 and prevalence 40.9/100,000; TCE prevalence was estimated at 4.1/100,000, projecting to 2,557 TCE patients in Italy. From 6,102 MM patients, 894 were identified as TCE; 887 had sufficient follow-up for inclusion. TCE patients had a mean age of 67 years and a mild comorbidity burden (Charlson Index = 0.7). Among 309 recent TCE cases (2022–2023), 35.6% became TCE in first-line therapy and 46.5% in second-line. HCRU analysis (n=461) showed high service use, with annual per-patient costs averaging €119,899—88% attributable to MM-related drugs. CONCLUSIONS: This real-world analysis highlights a growing population of TCE MM patients in Italy, with increasing exposure to combination therapies earlier in treatment. The findings underscore the substantial clinical and economic burden posed by this population, reinforcing the need for novel therapeutic options to improve outcomes and manage costs within the healthcare system.
format Article
id doaj-art-0aaaf87fc2a24078ba72334eeb7a0389
institution DOAJ
issn 2240-256X
language English
publishDate 2025-07-01
publisher SEEd Medical Publishers
record_format Article
series Farmeconomia: Health Economics and Therapeutic Pathways
spelling doaj-art-0aaaf87fc2a24078ba72334eeb7a03892025-08-20T02:44:24ZengSEEd Medical PublishersFarmeconomia: Health Economics and Therapeutic Pathways2240-256X2025-07-0126110.7175/fe.v26i1.15801376A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic BurdenValentina Perrone0Stefania Mazzoni1Maria Cappuccilli2Roberto Di Virgilio3Luca Degli Esposti4CliCon S.r.l. Società Benefit, Health, Economics & Outcomes Research, Bologna, ItalyCliCon S.r.l. Società Benefit, Health, Economics & Outcomes Research, Bologna, ItalyCliCon S.r.l. Società Benefit, Health, Economics & Outcomes Research, Bologna, ItalyPfizer Italia srl, Rome, ItalyCliCon S.r.l. Società Benefit, Health, Economics & Outcomes Research, Bologna, ItalyOBJECTIVES: This research aimed to provide updated epidemiological estimates of multiple myeloma (MM) in Italy and to characterize the clinical journey, treatment patterns, and economic burden focusing specifically on the subset of patients who have been exposed to all three major therapeutic classes: proteasome inhibitors, immunomodulatory drugs, and antiCD38 monoclonal antibodies (triple-class exposed, TCE). METHODS: A retrospective analysis was conducted using Italian healthcare administrative databases covering 12 million individuals. The research included (i) an epidemiological analysis of MM prevalence and incidence, and (ii) a longitudinal analysis of TCE patients identified between January 2017 and June 2023. Inclusion criteria required exposure to the three major MM drug classes. Healthcare resource utilization (HCRU) and direct costs from the Italian National Health Service perspective were assessed at one-year follow-up. RESULTS: As of August 2022, MM incidence was 9/100,000 and prevalence 40.9/100,000; TCE prevalence was estimated at 4.1/100,000, projecting to 2,557 TCE patients in Italy. From 6,102 MM patients, 894 were identified as TCE; 887 had sufficient follow-up for inclusion. TCE patients had a mean age of 67 years and a mild comorbidity burden (Charlson Index = 0.7). Among 309 recent TCE cases (2022–2023), 35.6% became TCE in first-line therapy and 46.5% in second-line. HCRU analysis (n=461) showed high service use, with annual per-patient costs averaging €119,899—88% attributable to MM-related drugs. CONCLUSIONS: This real-world analysis highlights a growing population of TCE MM patients in Italy, with increasing exposure to combination therapies earlier in treatment. The findings underscore the substantial clinical and economic burden posed by this population, reinforcing the need for novel therapeutic options to improve outcomes and manage costs within the healthcare system.https://journals.seedmedicalpublishers.com/index.php/FE/article/view/1580anti-cd38 monoclonal antibodiesdirect healthcare costsepidemiology estimatesimmunomodulatory drugsmultiple myelomaproteasome inhibitorsreal-world evidencetriple class-exposed patients
spellingShingle Valentina Perrone
Stefania Mazzoni
Maria Cappuccilli
Roberto Di Virgilio
Luca Degli Esposti
A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
Farmeconomia: Health Economics and Therapeutic Pathways
anti-cd38 monoclonal antibodies
direct healthcare costs
epidemiology estimates
immunomodulatory drugs
multiple myeloma
proteasome inhibitors
real-world evidence
triple class-exposed patients
title A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
title_full A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
title_fullStr A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
title_full_unstemmed A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
title_short A Real-World Analysis of Patients with Triple Class Exposed Multiple Myeloma in Italy: Epidemiology Estimates, Treatment Pattern and Economic Burden
title_sort real world analysis of patients with triple class exposed multiple myeloma in italy epidemiology estimates treatment pattern and economic burden
topic anti-cd38 monoclonal antibodies
direct healthcare costs
epidemiology estimates
immunomodulatory drugs
multiple myeloma
proteasome inhibitors
real-world evidence
triple class-exposed patients
url https://journals.seedmedicalpublishers.com/index.php/FE/article/view/1580
work_keys_str_mv AT valentinaperrone arealworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT stefaniamazzoni arealworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT mariacappuccilli arealworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT robertodivirgilio arealworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT lucadegliesposti arealworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT valentinaperrone realworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT stefaniamazzoni realworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT mariacappuccilli realworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT robertodivirgilio realworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden
AT lucadegliesposti realworldanalysisofpatientswithtripleclassexposedmultiplemyelomainitalyepidemiologyestimatestreatmentpatternandeconomicburden