Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051

Abstract Histone deacetylase 8 (HDAC8) is a well-known epigenetic regulator for cancer therapy. However, developing targeted inhibitors for HDAC8 is challenging due to a limited understanding of its structural dynamics, which is crucial for ligand interaction. Here, we employed an integrated approac...

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Main Authors: Yuxiang Luo, Zhaoyue Yan, Xiakun Chu, Ying Zhang, Yufan Qiu, Huilin Li
Format: Article
Language:English
Published: Nature Portfolio 2025-02-01
Series:Communications Biology
Online Access:https://doi.org/10.1038/s42003-025-07649-0
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author Yuxiang Luo
Zhaoyue Yan
Xiakun Chu
Ying Zhang
Yufan Qiu
Huilin Li
author_facet Yuxiang Luo
Zhaoyue Yan
Xiakun Chu
Ying Zhang
Yufan Qiu
Huilin Li
author_sort Yuxiang Luo
collection DOAJ
description Abstract Histone deacetylase 8 (HDAC8) is a well-known epigenetic regulator for cancer therapy. However, developing targeted inhibitors for HDAC8 is challenging due to a limited understanding of its structural dynamics, which is crucial for ligand interaction. Here, we employed an integrated approach, including native mass spectrometry (native MS), hydrogen-deuterium exchange mass spectrometry (HDX-MS), and molecular dynamics (MD) simulation, to investigate the inhibition mechanism and dynamic regulation of human HDAC8 (hHDAC8) by selective inhibitor PCI-34051, compared with the pan-inhibitor SAHA. Our results revealed that PCI-34051 engages with an expanded set of residues and conforms more aptly to the binding channel of hHDAC8, stabilizing the flexible loops surrounding the binding channel. Moreover, this dynamic stabilization effect is not limited to the binding regions, but also extends to distant regions (such as L2, α5, and α1 + α2), with L3 serving as a critical structural bridge. Overall, these results show the structural and dynamic regulations of hHDAC8 by PCI-34051, which induces a lower energy state for the protein-ligand system compared to SAHA, thus showing better inhibitory effects. In addition, it also suggests that certain regions, specifically loops L2 and L3, within the hHDAC8 protein could be key regions for targeted intervention.
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spelling doaj-art-06c261ff6c38438b97db78de58150dc72025-08-20T02:43:11ZengNature PortfolioCommunications Biology2399-36422025-02-018111110.1038/s42003-025-07649-0Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051Yuxiang Luo0Zhaoyue Yan1Xiakun Chu2Ying Zhang3Yufan Qiu4Huilin Li5School of Pharmaceutical Sciences, Sun Yat-sen University, No.132 Wai Huan Dong Lu, Guangzhou Higher Education Mega CenterCollege of Life Sciences, Zhejiang UniversityAdvanced Materials Thrust, The Hong Kong University of Science and Technology (Guangzhou)School of Pharmaceutical Sciences, Sun Yat-sen University, No.132 Wai Huan Dong Lu, Guangzhou Higher Education Mega CenterSchool of Pharmaceutical Sciences, Sun Yat-sen University, No.132 Wai Huan Dong Lu, Guangzhou Higher Education Mega CenterSchool of Pharmaceutical Sciences, Sun Yat-sen University, No.132 Wai Huan Dong Lu, Guangzhou Higher Education Mega CenterAbstract Histone deacetylase 8 (HDAC8) is a well-known epigenetic regulator for cancer therapy. However, developing targeted inhibitors for HDAC8 is challenging due to a limited understanding of its structural dynamics, which is crucial for ligand interaction. Here, we employed an integrated approach, including native mass spectrometry (native MS), hydrogen-deuterium exchange mass spectrometry (HDX-MS), and molecular dynamics (MD) simulation, to investigate the inhibition mechanism and dynamic regulation of human HDAC8 (hHDAC8) by selective inhibitor PCI-34051, compared with the pan-inhibitor SAHA. Our results revealed that PCI-34051 engages with an expanded set of residues and conforms more aptly to the binding channel of hHDAC8, stabilizing the flexible loops surrounding the binding channel. Moreover, this dynamic stabilization effect is not limited to the binding regions, but also extends to distant regions (such as L2, α5, and α1 + α2), with L3 serving as a critical structural bridge. Overall, these results show the structural and dynamic regulations of hHDAC8 by PCI-34051, which induces a lower energy state for the protein-ligand system compared to SAHA, thus showing better inhibitory effects. In addition, it also suggests that certain regions, specifically loops L2 and L3, within the hHDAC8 protein could be key regions for targeted intervention.https://doi.org/10.1038/s42003-025-07649-0
spellingShingle Yuxiang Luo
Zhaoyue Yan
Xiakun Chu
Ying Zhang
Yufan Qiu
Huilin Li
Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
Communications Biology
title Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
title_full Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
title_fullStr Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
title_full_unstemmed Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
title_short Binding mechanism and distant regulation of histone deacetylase 8 by PCI-34051
title_sort binding mechanism and distant regulation of histone deacetylase 8 by pci 34051
url https://doi.org/10.1038/s42003-025-07649-0
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