Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas

Abstract Background This study aimed to investigate the safety and efficacy of fourth-generation combined PSMA and GD2-targeted chimeric antigen receptor (CAR)-T cells in the treatment of refractory/relapsed gliomas. Method This study employed a single-arm design, enrolling patients with confirmed r...

Full description

Saved in:
Bibliographic Details
Main Authors: Jinshan Gu, Jiasheng Li, Yang Xu, Ge Zhang, Jingyi Xie, Rui Jia, Wei Chen, Zhengfeng Lu, Chengwei Chang, Haijun Wen, Lung-ji Chang, Huajuan Ma, Qichun Cai
Format: Article
Language:English
Published: BMC 2025-05-01
Series:Journal of Translational Medicine
Subjects:
Online Access:https://doi.org/10.1186/s12967-025-06523-1
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850111657627353088
author Jinshan Gu
Jiasheng Li
Yang Xu
Ge Zhang
Jingyi Xie
Rui Jia
Wei Chen
Zhengfeng Lu
Chengwei Chang
Haijun Wen
Lung-ji Chang
Huajuan Ma
Qichun Cai
author_facet Jinshan Gu
Jiasheng Li
Yang Xu
Ge Zhang
Jingyi Xie
Rui Jia
Wei Chen
Zhengfeng Lu
Chengwei Chang
Haijun Wen
Lung-ji Chang
Huajuan Ma
Qichun Cai
author_sort Jinshan Gu
collection DOAJ
description Abstract Background This study aimed to investigate the safety and efficacy of fourth-generation combined PSMA and GD2-targeted chimeric antigen receptor (CAR)-T cells in the treatment of refractory/relapsed gliomas. Method This study employed a single-arm design, enrolling patients with confirmed refractory/relapsed gliomas at the Immuno-oncology Department of the Cancer Center at Clifford Hospital in Guangdong. Eligible patients received combined treatment with PSMA CAR-T and GD2 CAR-T cells via intravenous administration. The dose of reinfused CAR-T cells ranged from 1–5 × 10^6 cells/kg of body weight. Results Six patients were included in the study, all of whom responded to the treatment. The overall response rate (ORR) was 50%, with three patients achieving complete response (CR) (50%) and three demonstrating stable disease (SD) (50%). The median progression-free survival (PFS) was 9.0 months (range, 1–56 months), and the median overall survival (OS) was 24.5 months (range, 13–63 months). Three patients (50%) developed cytokine release syndrome (CRS), all of which were classified as grade I CRS, and no patients experienced immune effector cell-associated neurotoxicity Syndrome (ICANS). Conclusion Combined PSMA CAR-T and GD2 CAR-T cell therapy demonstrated significant efficacy and good tolerability in the treatment of refractory/relapsed gliomas, without severe adverse reactions.
format Article
id doaj-art-03200e5bd4a04827bfacb689b883662f
institution OA Journals
issn 1479-5876
language English
publishDate 2025-05-01
publisher BMC
record_format Article
series Journal of Translational Medicine
spelling doaj-art-03200e5bd4a04827bfacb689b883662f2025-08-20T02:37:35ZengBMCJournal of Translational Medicine1479-58762025-05-0123111310.1186/s12967-025-06523-1Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomasJinshan Gu0Jiasheng Li1Yang Xu2Ge Zhang3Jingyi Xie4Rui Jia5Wei Chen6Zhengfeng Lu7Chengwei Chang8Haijun Wen9Lung-ji Chang10Huajuan Ma11Qichun Cai12Immuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalState Key Laboratory of Biocontrol, School of Life Sciences, Sun Yat-Sen UniversityState Key Laboratory of Biocontrol, School of Life Sciences, Sun Yat-Sen UniversityImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalShenzhen Geno-Immune Medical InstituteState Key Laboratory of Biocontrol, School of Life Sciences, Sun Yat-Sen UniversityShenzhen Geno-Immune Medical InstituteImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalImmuno-oncology department of the cancer center, 21 st Floor, Building 2, Guangdong Clifford HospitalAbstract Background This study aimed to investigate the safety and efficacy of fourth-generation combined PSMA and GD2-targeted chimeric antigen receptor (CAR)-T cells in the treatment of refractory/relapsed gliomas. Method This study employed a single-arm design, enrolling patients with confirmed refractory/relapsed gliomas at the Immuno-oncology Department of the Cancer Center at Clifford Hospital in Guangdong. Eligible patients received combined treatment with PSMA CAR-T and GD2 CAR-T cells via intravenous administration. The dose of reinfused CAR-T cells ranged from 1–5 × 10^6 cells/kg of body weight. Results Six patients were included in the study, all of whom responded to the treatment. The overall response rate (ORR) was 50%, with three patients achieving complete response (CR) (50%) and three demonstrating stable disease (SD) (50%). The median progression-free survival (PFS) was 9.0 months (range, 1–56 months), and the median overall survival (OS) was 24.5 months (range, 13–63 months). Three patients (50%) developed cytokine release syndrome (CRS), all of which were classified as grade I CRS, and no patients experienced immune effector cell-associated neurotoxicity Syndrome (ICANS). Conclusion Combined PSMA CAR-T and GD2 CAR-T cell therapy demonstrated significant efficacy and good tolerability in the treatment of refractory/relapsed gliomas, without severe adverse reactions.https://doi.org/10.1186/s12967-025-06523-1Refractory/relapsed gliomasPSMA CAR-T therapyGD2 CAR-T therapyCombination therapy
spellingShingle Jinshan Gu
Jiasheng Li
Yang Xu
Ge Zhang
Jingyi Xie
Rui Jia
Wei Chen
Zhengfeng Lu
Chengwei Chang
Haijun Wen
Lung-ji Chang
Huajuan Ma
Qichun Cai
Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
Journal of Translational Medicine
Refractory/relapsed gliomas
PSMA CAR-T therapy
GD2 CAR-T therapy
Combination therapy
title Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
title_full Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
title_fullStr Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
title_full_unstemmed Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
title_short Preliminary exploration of PSMA CAR-T combined with GD2 CAR-T for the treatment of refractory/relapsed gliomas
title_sort preliminary exploration of psma car t combined with gd2 car t for the treatment of refractory relapsed gliomas
topic Refractory/relapsed gliomas
PSMA CAR-T therapy
GD2 CAR-T therapy
Combination therapy
url https://doi.org/10.1186/s12967-025-06523-1
work_keys_str_mv AT jinshangu preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT jiashengli preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT yangxu preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT gezhang preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT jingyixie preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT ruijia preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT weichen preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT zhengfenglu preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT chengweichang preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT haijunwen preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT lungjichang preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT huajuanma preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas
AT qichuncai preliminaryexplorationofpsmacartcombinedwithgd2cartforthetreatmentofrefractoryrelapsedgliomas