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Real-world clinical outcomes of patients with CLN2 disease treated with cerliponase alfa by Angela Schulz, Angela Schulz, Christoph Schwering, Eva Wibbeler, Lena Marie Westermann, Luca Hagenah, Susanne Lezius, Ashok Jha, Abigail Hunt, Peter Slasor, Pascal Reisewitz, Miriam Nickel
Published 2025-03-01Get full text
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