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Demographics, clinical characteristics, and real-world treatment patterns among patients with beta-thalassemia: a retrospective medical record abstraction study by Maria Domenica Cappellini, Mrudula B. Glassberg, Juliana Meyers, Maria Jimenez, Tram Nham, Luciana Bueno, Jan Sieluk, Aylin Yucel, Ferras Alashkar
Published 2024-12-01Get full text
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Identifying thresholds for meaningful improvements in NTDT-PRO scores to support conclusions about treatment benefit in clinical studies of patients with non-transfusion-dependent... by Ali T Taher, Maria Domenica Cappellini, Khaled M Musallam, Vip Viprakasit, Antonis Kattamis, Jennifer Lord-Bessen, Aylin Yucel, Shien Guo, Alan L Shields, Jeevan K Shetty, Luciana Moro Bueno, Christopher G Pelligra, Mrudula B Glassberg
Published 2024-11-01Get full text
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