Psychometric analysis of the patient-reported outcomes measurement information system parent proxy physical function–upper extremity item bank for children with Duchenne muscular d... by Linda Pax Lowes, Corinne M. Le Reun, Teofil Ciobanu, Lindsay N. Alfano, Natalie F. Reash, Megan A. Iammarino, Shivangi Patel, Ivana F. Audhya

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Validity and Reliability of Clinical and Patient‐Reported Outcomes in Multisystem Proteinopathy 1 by Lindsay N. Alfano, Megan A. Iammarino, Natalie F. Reash, Linda P. Lowes, Lindsay Pietruszewski, Kathleen Adderley, Lauren Humphrey, Audrey B. Knight, Christopher L. Steiner, Melissa A. Smith, Zarife Sahenk, Anne M. Connolly, Momen Almomen, Eleonora S. D'Ambrosio, Nathan Peck, Allison Peck

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Clinical Trial Readiness in Limb Girdle Muscular Dystrophy R1 (LGMDR1): A GRASP Consortium Study by Stephanie M. Hunn, Lindsay N. Alfano, Aileen Jones, Amanda Butler, Linda P. Lowes, Megan A. Iammarino, Natalie F. Reash, Lindsay Pietruszewski, Sandhya Sasidharan, Melissa Currence, Jeffrey M. Statland, Talia Strahler, Robert Will, Matthew Wicklund, Stacy Dixon, Renee Augsburger, Tahseen Mozaffar, Katie M. Laubscher, Shelley R. H. Mockler, Katherine D. Mathews, Nikia Stinson, Doris G. Leung, Molly M. Stark, Rebecca A. Horton, Peter B. Kang, Meredith K. James, Amanda Clause, Conrad C. Weihl, Nicholas E. Johnson, GRASP‐LGMD Consortium

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Prospective observational study of FKRP‐related limb‐girdle muscular dystrophy R9: A GRASP consortium study by Lindsay N. Alfano, Meredith K. James, Kristine Grosfjeld Petersen, Karen Rudolf, John Vissing, Renee Augsburger, Tahseen Mozaffar, Aileen Jones, Amanda Butler, Katie M. Laubscher, Shelley R. H. Mockler, Katherine D. Mathews, Megan A. Iammarino, Natalie F. Reash, Lindsay Pietruszewski, Linda P. Lowes, Talia Strahler, Matthew Wicklund, Stephanie Hunn, Conrad C. Weihl, Sandhya Sasidharan, Melissa Currence, Jeffrey M. Statland, Nikia Stinson, Megan Holzer, Doris G. Leung, Donovan J. Lott, Peter B. Kang, Scott Holsten, Urvi Desai, Nicholas E. Johnson, the GRASP‐LGMD Consortium

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