P281: JOURNEY: A natural history study of limb-girdle muscular dystrophies R3–R5, baseline characteristics of study cohort by Linda P. Lowes, Carlos Ortez Gonzalez, Kristl Claeys, Chamindra Laverty, Andrea Gangfuss, Crystal Proud, Jordi Diaz Manera, Meredith James, Lindsay Alfano, Herb Stevenson, Lixi Yu, André Mueller-York, Giacomo Comi

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Validity and Reliability of Clinical and Patient‐Reported Outcomes in Multisystem Proteinopathy 1 by Lindsay N. Alfano, Megan A. Iammarino, Natalie F. Reash, Linda P. Lowes, Lindsay Pietruszewski, Kathleen Adderley, Lauren Humphrey, Audrey B. Knight, Christopher L. Steiner, Melissa A. Smith, Zarife Sahenk, Anne M. Connolly, Momen Almomen, Eleonora S. D'Ambrosio, Nathan Peck, Allison Peck

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Clinical Trial Readiness in Limb Girdle Muscular Dystrophy R1 (LGMDR1): A GRASP Consortium Study by Stephanie M. Hunn, Lindsay N. Alfano, Aileen Jones, Amanda Butler, Linda P. Lowes, Megan A. Iammarino, Natalie F. Reash, Lindsay Pietruszewski, Sandhya Sasidharan, Melissa Currence, Jeffrey M. Statland, Talia Strahler, Robert Will, Matthew Wicklund, Stacy Dixon, Renee Augsburger, Tahseen Mozaffar, Katie M. Laubscher, Shelley R. H. Mockler, Katherine D. Mathews, Nikia Stinson, Doris G. Leung, Molly M. Stark, Rebecca A. Horton, Peter B. Kang, Meredith K. James, Amanda Clause, Conrad C. Weihl, Nicholas E. Johnson, GRASP‐LGMD Consortium

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Prospective observational study of FKRP‐related limb‐girdle muscular dystrophy R9: A GRASP consortium study by Lindsay N. Alfano, Meredith K. James, Kristine Grosfjeld Petersen, Karen Rudolf, John Vissing, Renee Augsburger, Tahseen Mozaffar, Aileen Jones, Amanda Butler, Katie M. Laubscher, Shelley R. H. Mockler, Katherine D. Mathews, Megan A. Iammarino, Natalie F. Reash, Lindsay Pietruszewski, Linda P. Lowes, Talia Strahler, Matthew Wicklund, Stephanie Hunn, Conrad C. Weihl, Sandhya Sasidharan, Melissa Currence, Jeffrey M. Statland, Nikia Stinson, Megan Holzer, Doris G. Leung, Donovan J. Lott, Peter B. Kang, Scott Holsten, Urvi Desai, Nicholas E. Johnson, the GRASP‐LGMD Consortium

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