Case Report: Eltrombopag in mosaic and gene therapy-treated patients with Fanconi anemia by Josune Zubicaray, June Iriondo, Elena Sebastián, Alejandro Sanz, Paula Rio, Jean Soulier, Sonsoles San Román, José J. Uriz, Susana Navarro, Eileen Nicoletti, Juan A. Bueren, Jonathan D. Schwartz, Julián Sevilla

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Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patients by Begoña Diez, Pietro Genovese, Francisco J Roman‐Rodriguez, Lara Alvarez, Giulia Schiroli, Laura Ugalde, Sandra Rodriguez‐Perales, Julian Sevilla, Cristina Diaz de Heredia, Michael C Holmes, Angelo Lombardo, Luigi Naldini, Juan Antonio Bueren, Paula Rio

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