Phase 2a/b randomised placebo-controlled dose-escalation trial of triheptanoin for ataxia-telangiectasia: treating mitochondrial dysfunction with anaplerosisResearch in context by Matthew Lynch, Sophie Manoy, Peter D. Sly, Claire E. Wainwright, Ernst Wolvetang, John E. Feenstra, Jason Dowling, Robert S. Ware, Maharshi S. Patel, Diana Hermith-Ramirez, Adam Vogel, Kahn Preece, Tania Zappala, Shuan Dai, Ann Webber, Abrey Yeo, Goutham Subramanian, Geetha Rao, Cindy S. Ma, Sara Jose, Magtouf Gatei, Bowen Xin, Nicoletta Sandona, Peter Lewindon, Katherine G. Sinclair, Sam Nayler, Martin F. Lavin, David J. Coman

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