Showing 1 - 3 results of 3 for search 'Fulvio Mavilio', query time: 0.02s
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Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity by Michelle Eggers, Charles H Vannoy, Jianyong Huang, Pravinkumar Purushothaman, Jacqueline Brassard, Carlos Fonck, Hui Meng, Mariah J Prom, Michael W Lawlor, Justine Cunningham, Chanchal Sadhu, Fulvio Mavilio
Published 2021-12-01Get full text
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A single epidermal stem cell strategy for safe ex vivo gene therapy by Stéphanie Droz‐Georget Lathion, Ariane Rochat, Graham Knott, Alessandra Recchia, Danielle Martinet, Sara Benmohammed, Nicolas Grasset, Andrea Zaffalon, Nathalie Besuchet Schmutz, Emmanuelle Savioz‐Dayer, Jacques Samuel Beckmann, Jacques Rougemont, Fulvio Mavilio, Yann Barrandon
Published 2015-02-01Get full text
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