Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer by Marine Laurent, Rim Harb, Christine Jenny, Julie Oustelandt, Simon Jimenez, Jeremie Cosette, Francesca Landini, Aristide Ferrante, Guillaume Corre, Nemanja Vujic, Claudia Piccoli, Anais Brassier, Laetitia Van Wittenberghe, Giuseppe Ronzitti, Dagmar Kratky, Consiglia Pacelli, Mario Amendola

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