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Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome by Valentina Vavassori, Elisabetta Mercuri, Genni E Marcovecchio, Maria C Castiello, Giulia Schiroli, Luisa Albano, Carrie Margulies, Frank Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola MV Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan Lankester, Francesca Ferrua, Eugenio Scanziani, Cecilia Cotta‐Ramusino, Anna Villa, Luigi Naldini, Pietro Genovese
Published 2021-01-01Get full text
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Long-term outcome in Wiskott-Aldrich syndrome and X-linked thrombocytopenia patients: an observational -prospective multi-center study of the Italian Primary Immune Deficiency Netw... by Annarosa Soresina, Roberto Rondelli, Lucia Dora Notarangelo, Franco Locatelli, Alessandro Aiuti, Alessandra Biffi, Marco Rabusin, Claudio Pignata, Giuseppe Menna, Arcangelo Prete, Maura Faraci, Attilio Rovelli, Francesca Conti, Patrizia Bertolini, Chiara Azzari, Caterina Cancrini, Marco Zecca, Francesca Ferrua, Maria Pia Cicalese, Francesco Cecere, Laura Dotta, Baldassarre Martire, Silvia Giliani, Daniele Moratto, Cinzia Mazza, Alessandro Plebani, Luigi D. Notarangelo, Andrea Pession, Raffaele Badolato, Fulvio Fulvio
Published 2025-06-01Get full text
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