The relationship between adult phenylketonuria and the cardiovascular system - insights into mechanisms and risks by Yann Dos Santos, Friedrich Trefz, Maria Giżewska, Annemiek M.J. van Wegberg, Bruno Lefort, François Labarthe, Francjan van Spronsen, François Maillot

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Pantethine therapy dramatically rescues end‐stage failing heart in a patient with deficiency of coenzyme A biosynthesis by Violette Goetz, Bruno Lefort, Magalie Barth, Naïg Gueguen, Céline Bris, Emmanuelle Blanchard, Isabelle Benz‐de Bretagne, Hélène Blasco, Marine Tardieu, François Labarthe

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Immunization coverage and timeliness of vaccination in young patients with inborn errors of metabolism: a French multicentric study by Anne-Sophie Renous, Lena Damaj, Magali Gorce, Magalie Barth, Antoine Bedu, Elise Sacaze, Delphine Lamireau, Cécile Laroche-Raynaud, Laurent Pasquier, Zoha Maakaroun-Vermesse, Marine Tardieu, François Labarthe

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