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Blocking sense‐strand activity improves potency, safety and specificity of anti‐hepatitis B virus short hairpin RNA by Thomas Michler, Stefanie Große, Stefan Mockenhaupt, Natalie Röder, Ferdinand Stückler, Bettina Knapp, Chunkyu Ko, Mathias Heikenwalder, Ulrike Protzer, Dirk Grimm
Published 2016-07-01Get full text
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Clinically translatable mitochondrial gene therapy in muscle using tandem mtZFN architecture by Pavel A Nash, Keira M Turner, Christopher A Powell, Lindsey Van Haute, Pedro Silva-Pinheiro, Felix Bubeck, Ellen Wiedtke, Eloïse Marques, Dylan G Ryan, Dirk Grimm, Payam A Gammage, Michal Minczuk
Published 2025-04-01Get full text
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